ATLAS: A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, ADAPTIVE SEAMLESS PHASE 2/3 STUDY TO ASSESS THE SAFETY AND EFFICACY OF MOMELOTINIB IN PATIENTS WITH VEXAS SYNDROME
EHA Library, David Beck,
4209713
REAL-WORLD PHYSICIANS AND PATIENTS PERSPECTIVES ON ADHERENCE, SATISFACTION WITH PEGCETACOPLAN, AND HEALTH RELATED QUALITY OF LIFE ACROSS EUROPE, THE UNITED STATES AND CANADA: A CROSS-SECTIONAL STUDY
EHA Library, Jens Panse,
4209682
SAFETY, PHARMACOKINETICS, AND PHARMACODYNAMICS OF MY008211A, AN ORAL COMPLEMENT FACTOR B INHIBITOR, IN SINGLE- AND MULTIPLE-ASCENDING-DOSE STUDIES IN HEALTHY PARTICIPANTS
EHA Library, Xin Li,
4209683
INCIDENCE RATES OF SERIOUS INFECTIONS IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA: A REAL-WORLD COMPARISON USING DATA FROM TRINETX ACROSS THE US, EUROPE, AND OTHER REGIONS
EHA Library, Håkan Malmström,
4209689
FIRST-IN-HUMAN, FIRST-IN-PATIENT STUDY OF ALN-CFB, AN INVESTIGATIONAL SIRNA TARGETING HEPATIC COMPLEMENT FACTOR B: TREATMENT OF PERSISTENT ANEMIA IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA
EHA Library, Nikhil Singh,
4209701