SINGLE ASCENDING DOSES OF 9MW3011, A MONOCLONAL ANTIBODY TARGETING TMPRSS6, RESULT IN SUSTAINED ELEVATION OF SERUM HEPCIDIN AND REDUCTION OF IRON LEVELS IN HEALTHY VOLUNTEERS
EHA Library, Jie Hou,
419655
SINGLE ASCENDING DOSES OF REGN7999, A MONOCLONAL ANTIBODY INHIBITOR OF TMPRSS6, INCREASED SERUM HEPCIDIN AND CAUSED DEEP, SUSTAINED REDUCTIONS IN SERUM IRON IN HEALTHY HUMAN VOLUNTEERS
EHA Library, Nikhil Singh,
419658
TOPLINE RESULTS OF THE AURORA TRIAL: A PHASE 2, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED TRIAL OF BITOPERTIN IN ERYTHROPOIETIC PROTOPORPHYRIA
EHA Library, Amy Dickey,
419662
SOVLEPLENIB IN PRIMARY IMMUNE THROMBOCYTOPENIA (ITP) PATIENTS BY PRIOR LINES OF THERAPY: SUBGROUP ANALYSIS OF A MULTICENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED PHASE 3 STUDY (ESLIM-01)
EHA Library, Xiaofan Liu,
419716
INCIDENCE, DESCRIPTION, AND MANAGEMENT OF VENOUS THROMBOSES IN ADULT PATIENTS WITH IMMUNE THROMBOCYTOPENIC PURPURA. RESULTS FROM THE MULTICENTER PROSPECTIVE REGISTRY CARMEN-FRANCE.
EHA Library, François THERME,
419717
SOVLEPLENIB IN PRIMARY IMMUNE THROMBOCYTOPENIA (ITP) PTS WITH PRIOR TPO/TPO-RA TREATMENT: SUBGROUP ANALYSIS OF A MULTICENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED PHASE 3 STUDY (ESLIM-01)
EHA Library, Heng Mei,
419718
LONG-TERM SAFETY AND EFFICACY OF RILZABRUTINIB, AN ORAL BRUTON TYROSINE KINASE INHIBITOR, IN PATIENTS WITH IMMUNE THROMBOCYTOPENIA (ITP): INTEGRATED PHASE 2 PART A AND PART B
EHA Library, Nichola Cooper,
419722
INDIVIDUAL PHARMACOKINETIC EVALUATION OF FIXED-SEQUENCE SINGLE-DOSE OCTOCOG ALFA, RURIOCTOCOG ALFA PEGOL, AND EFANESOCTOCOG ALFA IN ADULTS WITH SEVERE HEMOPHILIA A
EHA Library, Jimenez Yuste Victor ,
419732