RENI-CEL, THE FIRST ASCAS12A GENE-EDITED CELL THERAPY, SHOWS PROMISING PRELIMINARY RESULTS IN KEY CLINICAL OUTCOMES IN TRANSFUSION-DEPENDENT BETA-THALASSEMIA PATIENTS TREATED IN THE EDITHAL TRIAL
EHA Library, Haydar Frangoul,
419563
ADHERENCE, TREATMENT USE, AND CLINICAL OUTCOMES IN PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VASO-OCCLUSIVE CRISES TREATED WITH L-GLUTAMINE, VOXELOTOR, OR CRIZANLIZUMAB IN THE UNITED STATES
EHA Library, Chuka Udeze,
419570
CHANGES IN PHYSICAL, MENTAL, AND SOCIAL HEALTH OF ADULTS WITH SICKLE CELL DISEASE FOLLOWING ALLOGENEIC STEM CELL TRANSPLANTATION: A MIXED-METHODS, PROSPECTIVE COHORT STUDY
EHA Library, Elisabeth Dovern,
419572
INCREASED RISK OF OSTEOARTHRITIS IN HFE C282Y HOMOZYGOUS INDIVIDUALS WITH NORMAL LEVELS OF IRON, TRANSFERRIN SATURATION, OR FERRITIN: A PROSPECTIVE STUDY OF 132,529 GENERAL POPULATION INDIVIDUALS
EHA Library, Jens Helby,
419647