A PHASE 2, MULTICENTER, SINGLE-ARM STUDY TO EVALUATE SAFETY AND EFFICACY OF DEFERASIROX AFTER HEMATOPOIETIC STEM CELL TRANSPLANTATION IN CHILDREN WITH BETA-THALASSEMIA MAJOR
EHA Library, Mehmet Akif Yesilipek,
133066
ALXN1210, A LONG-ACTING C5 INHIBITOR, RESULTS IN RAPID AND SUSTAINED REDUCTION OF LDH WITH A MONTHLY DOSING INTERVAL IN PATIENTS WITH PNH: PRELIMINARY DATA FROM A DOSE-ESCALATION STUDY
EHA Library, Jong Wook Lee,
135358