ACTIVATE: A PHASE 3, RANDOMIZED, MULTICENTER, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY OF AG-348 IN ADULTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED
EHA Library, Marie-Hélène Jouvin,
214855
RESULTS OF A DOSE ESCALATION STUDY OF ME-401, A SELECTIVE PI3KΔ INHIBITOR, IN RELAPSED/REFRACTORY (R/R) FOLLICULAR LYMPHOMA (FL) AND CHRONIC LYMPHOCYTIC LEUKEMIA (CLL)/SMALL LYMPHOCYTIC LYMPHOMA (SLL)
EHA Library, John M Pagel,
214903
LONG TERM INTEGRATED SAFETY ANALYSIS OF UMBRALISIB (TGR-1202), A PI3K-DELTA/CK1-EPSILON INHIBITOR WITH A DIFFERENTIATED SAFETY PROFILE, IN PATIENTS WITH RELAPSED/REFRACTORY LYMPHOID MALIGNANCIES
EHA Library, Matthew S. Davids, MD, MMSC,
214906
A PHASE 1, PLACEBO-CONTROLLED STUDY TO DETERMINE THE SAFETY, TOLERABILITY, AND PHARMACOKINETICS OF ESCALATING SUBCUTANEOUS DOSES OF LJPC-401 (SYNTHETIC HUMAN HEPCIDIN) IN HEALTHY ADULTS
EHA Library, Antonis Kattamis,
214932
AN OPEN-LABEL, MULTICENTER, SINGLE-ARM, PHASE II STUDY ASSESSING PATIENT PREFERENCE FOR THE DEFERASIROX FILM-COATED TABLET COMPARED TO THE REFERENCE DISPERSIBLE TABLET FORMULATION: THE JUPITER STUDY
EHA Library, Vip Viprakasit,
214937