TRIAL IN PROGRESS: A RANDOMIZED, OPEN-LABEL, PHASE 3 STUDY OF AXATILIMAB VERSUS BEST AVAILABLE THERAPY IN PATIENTS WITH CHRONIC GRAFT-VERSUS-HOST DISEASE AFTER ≥2 PRIOR LINES OF SYSTEMIC THERAPY
EHA Library, Mi Kwon, 4159502
EVALUATING RUXOLITINIB TOXICITY IN PEDIATRIC PATIENTS WITH STEROID REFRACTORY GRAFT-VERSUS-HOST DISEASE: A SINGLE-CENTER EXPERIENCE
EHA Library, Mennatallah Elnaggar, 4159503
AUTOLOGOUS VS. ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR T-CELL LYMPHOBLASTIC LYMPHOMA:ALLOGENEIC TRANSPLANTATION---A PREFERENTIAL SELECTION, BUT NO SIGNIFICANT ADVANTAGES
EHA Library, Haiwen Huang, 4159504
OUTCOMES OF ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANT (ALLO-HSCT) IN ADULTS WITH HEREDITARY MYELOID MALIGNANCIES, A SINGLE-CENTER STUDY
EHA Library, Amagoia Ruiz Martin, 4159505
OPTIMIZATION AND EFFICACY OF FULL-DOSE RECOMBINANT HUMAN THROMBOPOIETIN IN PLATELET ENGRAFTMENT AFTER ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION: A REAL-WORLD RETROSPECTIVE STUDY
EHA Library, Shiyu Chen, 4159506
REDUCED INTENSITY T-REPLETE ALLOGENEIC TRANSPLANT CAN PROVIDE LONG TERM SURVIVAL IN PATIENTS WITH ANGIOIMMUNOBLASTIC T CELL LYMPHOMA ABOVE THE AGE OF 50 WHO PREVIOUSLY HAD AUTOLOGOUS STEM CELL TRANSPLANTATION
EHA Library, Ioannis Arvanitis, 4159507
IMMUNOLOGIC PREDICTIVE FACTORS FOR CMV REACTIVATION IN SR-CGVHD PATIENTS TREATED WITH RUXOLITINIB
EHA Library, Leonardo Maia Moço, 4159508
A SINGLE CENTRE EXPERIENCE OF USING BELUMOSUDIL FOR THE TREATMENT OF CHRONIC GRAFT VERSUS HOST DISEASE
EHA Library, Catherine Garnett, 4159509
INFLUENCE OF BODY MASS INDEX (BMI) ON OUTCOMES AND TOXICITY ASSOCIATED WITH CHIMERIC ANTIGEN RECEPTOR T-CELL THERAPY (CAR-T): A SINGLE-CENTRE DATA SET FROM THE ROYAL MARSDEN HOSPITAL
EHA Library, Ellouise Bishop, 4159510
THREE-MONTH WHOLE BLOOD CHIMERISM INDEPENDENTLY PREDICTS OVERALL SURVIVAL IN ALLOGENEIC STEM CELL TRANSPLANTS FOR HEMATOLOGICAL CANCERS: AN ANALYSIS ON BEHALF OF TWO UK CENTRES
EHA Library, Rebecca Goodhew, 4159511
BELUMOSUDIL FOR CHRONIC GRAFT-VERSUS-HOST DISEASE: A SYSTEMATIC REVIEW AND META-ANALYSIS
EHA Library, Kristin Rathje, 4159512
A SINGLE RIBOSOMAL RNA METHYLATION IS ESSENTIAL FOR HEMATOPOIETIC STEM CELL FITNESS
EHA Library, Daphna Nachmani, 4159513
DISTINCT TRANSCRIPTIONAL CHANGES IN DIFFERENT MURINE MULTIPOTENT PROGENITORS DURING EMERGENCY GRANULOPOIESIS
EHA Library, Srdjan Grusanovic, 4159514
CHANGES IN GLUTAMINE AVAILABILITY DRIVE HAEMATOPOIETIC STEM CELL AGEING
EHA Library, Charlotte Hellmich, 4159515
A NOVEL 'PLATELET PROTOCOL' TARGETS CYTOKINE STORM IN HEMOPHAGOCYTIC LYMPHOHISTIOCYTOSIS
EHA Library, Zhenyu Liu, 4159516
ADAPTIVE IMMUNITY GOVERNS THE CLEARANCE OF ONCOGENE-INDUCED SENESCENT HSPCS AND CONTROLS INFLAMMATION
EHA Library, Cristina Colleoni, 4159517
LOSS OF HFE IMPAIRS HEMATOPOIETIC STEM AND PROGENITOR CELL FUNCTION
EHA Library, Liliana Arede, 4159518
GENETIC LANDSCAPE OF DNMT3A- AND TET2-DRIVEN CLONAL HAEMATOPOIESIS IN TWO MOUSE MODELS
EHA Library, Clea Barcena, 4159519
CONDITIONAL DELETION OF RIBOSOMAL PROTEIN SUBUNITS HIGHLIGHTS THEIR SPECIFIC REQUIREMENTS DURING FETAL HEMATOPOIESIS
EHA Library, Lionel Blanc, 4159520
TNIK IS A CRITICAL REGULATOR OF HSC MAINTENANCE AND DIFFERENTIATION
EHA Library, Luca Palombella, 4159521
DISRUPTED VCAM-1/VLA-4 INTERACTION CONTRIBUTES TO IMPAIRED ADHESION OF SPECIFIC HEMATOPOIETIC STEM AND PROGENITOR CELL SUBPOPULATIONS IN THE BONE MARROW, ULTIMATELY LEADING TO LEUKEMOGENESIS
EHA Library, Shlomit Yehudai-Reshef, 4159522
CHARACTERIZATION OF PD-L1 AS NOVEL THERAPEUTIC TARGET IN MASTOCYTOSIS
EHA Library, Elena Ratti, 4159523
THE HPG-IMMUNE CROSSTALK SHAPES THE SEX-SPECIFIC HUMAN IMMUNE LANDSCAPE ACROSS THE LIFESPAN
EHA Library, Andrea Hanel, 4159524
TREATMENT OUTCOME AND EFFICACY OF DESENSITIZATION STRATEGIES FOR IMMUNIZED-PTR IN HEMATOLOGICAL MALIGNANCIES BEFORE HEMATOPOIETIC STEM CELL TRANSPLANTATION
EHA Library, Xiaowen Tang, 4159525
SINGLE CELL ANALYSIS REVEALS A DISTINCT TRANSCRIPTOME SIGNATURE OF HUMAN HEMATOPOIETIC STEM AND PROGENITOR CELLS UNDER CHEMOTHERAPY STRESS IN B-ALL
EHA Library, Xiaoli Chen, 4159526
MBD4 KNOCKOUT AS A TOOL FOR MODELLING MUTAGENESIS AND CLONAL OUTGROWTH
EHA Library, Sanne Massaar, 4159527
POT1 GERMLINE MUTATIONS IN LONG TELOMERE SYNDROME: IMPLICATIONS FOR CANCER RISK AND CLONAL HEMATOPOIESIS
EHA Library, Madeline Franke, 4159528
PIEZO1 DELAYS HUMAN ERYTHROCYTE DIFFERENTIATION THROUGH PHOSPHORYLATION AND DEGRADATION OF CALPASTATIN
EHA Library, Alexandre Willaume, 4159529
SINGLE-CELL MULTIOMICS OF PEDIATRIC BONE MARROW REVEALS AGE-DEPENDENT DIFFERENCES IN LINEAGE DIFFERENTIATION
EHA Library, Evelyn Hanemaaijer, 4159530
FUNCTIONAL VALIDATION OF THE ROLE OF GERMLINE VARIATION IN CLONAL HAEMATOPOIESIS
EHA Library, Michela Colombo, 4159531
SPONTANEOUSLY CIRCULATING HEMATOPOIETIC STEM/PROGENITOR CELLS AT SINGLE CELL RESOLUTION: LESSONS FROM A RARE BONE DISEASE
EHA Library, Valentina Capo, 4159532
HYPUSINATION-MEDIATED REGULATION OF MURINE ERYTHROPOIESIS IS ASSOCIATED WITH ALTERATIONS IN AUTOPHAGY
EHA Library, Pedro Gonzalez-Menendez, 4159533
DISTINCT ONTOGENETIC LINEAGES DICTATE CDC2 HETEROGENEITY
EHA Library, Carlos Minutti, 4159534
STEM CELL ENLARGEMENT - A NEW HALLMARK OF AGING?
EHA Library, Jette Lengefeld, 4159535
A BISPECIFIC ANTI-FLUORESCEIN X ANTI-CD3 T-CELL ENGAGER ANTIBODY IN COMBINATION WITH FLUORESCEINATED ADAPTORS ENABLES LYSIS OF NEOPLASTIC CELLS
EHA Library, Laura Volta, 4159537
SENESCENCE AND INFLAMMATION ARE UNINTENDED ADVERSE CONSEQUENCES OF CRISPR-CAS9/AAV6 MEDIATED GENE EDITING IN HEMATOPOIETIC STEM CELLS
EHA Library, Anastasia Conti, 4159538
SYSTEMIC INFLAMMATION MODULATES CAR T-CELL EXPANSION AND RESPONSE IN RELAPSED/REFRACTORY LARGE B-CELL LYMPHOMAS
EHA Library, Sadhana Jonnalagadda, 4159539
HARNESSING CMV-VSTS FOR ALLOGENEIC CART84 THERAPY TO TARGET AML
EHA Library, Maria Val Casals, 4159540
EX VIVO EXPANDED HSCS IMPROVE GENE THERAPY OUTCOME IN AUTOSOMAL RECESSIVE OSTEOPETROSIS
EHA Library, Valeria Iannello, 4159541
IN VIVO LENTIVIRAL VECTOR GENE TRANSFER INTO HEMATOPOIETIC STEM AND PROGENITOR CELLS
EHA Library, Michela Milani, 4159542
MZB1-DIRECTED HLA-DEPENDENT CAR T CELLS FOR TARGETING B-CELL MALIGNANCIES
EHA Library, Elena Maroto Martín, 4159543
MULTIMODAL ANALYSES INDICATE TREATMENT-NAIVE T CELLS AS A SUPERIOR SOURCE OF CAR T-CELLS IN LYMPHOMA PATIENTS
EHA Library, Il-Kang Na, 4159544
SINGLE-CELL PROFILING OF HAEMATOPOIETIC STEM CELL COLLECTION COMPOSITION AND ITS IMPACT ON POST-TREATMENT HAEMATOTOXICITY
EHA Library, li guangmei, 4159545
DISSECTING THE ROLE OF AFFINITY IN TROGOCYTOSIS OF ANTI-CD19 CAR T-CELLS
EHA Library, Claudia D'oria, 4159546
BASE EDITING OF HEMATOPOIETIC STEM CELLS AND T CELLS RESTORES PI3K SIGNALLING IN APDS1 AND APDS2 PATIENTS
EHA Library, Kate Orf, 4159547
HDR GENE CORRECTION AND SELECTION OF CD4+ T CELLS FOR THE TREATMENT OF HYPER IGM1: MOVING TOWARD AN ACADEMIC CLINICAL TRIAL
EHA Library, Daniele Canarutto, 4159549
THE STUDY ON THE EFFECTS AND MECHANISMS OF TYROSINE KINASE INHIBITORS ON THE FUNCTION OF CD19 CAR-T CELLS
EHA Library, Rong Xie, 4159550
ADVANCING NK CELL-DERIVED EXTRACELLULAR VESICLES TOWARDS A CLINICAL-GRADE IMMUNOTHERAPY PRODUCT FOR HEMATOLOGICAL MALIGNANCIES
EHA Library, Aladin Samara, 4159551
EXPANSION OF FUNCTIONAL MEMORY NK CELLS FROM CMV-POSITIVE AND -NEGATIVE DONORS USING LEUKEMIC-DERIVED DENDRITIC CELLS
EHA Library, Satwinder Kaur Singh, 4159552
IMPROVING THE ANTITUMOR EFFICACY OF CAR-BASED CELLULAR IMMUNOTHERAPIES VIA TARGETING AN IMMUNITY NEGATIVE REGULATOR
EHA Library, Yue Liu, 4159553
DEVELOPMENT OF POLYMER-BASED NANOVECTORS FOR IN VIVO DELIVERY OF MRNA-THERAPEUTICS FOR PRIMARY MYELOFIBROSIS
EHA Library, Anna Rita Franco Migliaccio, 4159554
BIOLOGICAL PROPERTIES AND CLONALITY OF ENGINEERED HEMATOPOIETIC STEM/PROGENITOR CELLS PERSISTING LONG-TERM AFTER GENE THERAPY
EHA Library, Serena Scala, 4159555
A NOVEL CANCER VACCINE BASED ON HYALURONIC ACID NANOGEL (HANG) IMPROVES THE NUMBER AND FUNCTIONS OF INFUSED TCR-T CELLS, ESPECIALLY INDUCES „ANTIGEN-SPREADING”, RESULTING IN LONG-TERM CURE OF IMMUNOTHERAPY-RESISTANT SOLID TUMORS
EHA Library, Fumiyasu Momose, 4159556
FORMATION OF TUNNELING NANOTUBES IN CHRONIC LYMPHOCYTIC LEUKEMIA AND ASSOCIATED MITOCHONDRIAL TRANSFER TRIGGER (CAR)-T CELL EXHAUSTION
EHA Library, Michal Smida, 4159557
CXCR4-R334X MOUSE: A MODEL TO INVESTIGATE THE PATHOGENESIS OF WHIM SYNDROME AND ASSESS NOVEL GENE CORRECTION THERAPY
EHA Library, Alessandra Zecchillo, 4159558
SUCCESSFUL GENERATION OF IPSC-DERIVED TH1 CELLS WHICH ENHANCED CD8+ CAR-T CELL FUNCTION
EHA Library, Yoshiki Furukawa, 4159559
ANTI-CD19 CAR T-CELL THERAPY FOR HLA DESENSITIZATION IN A HIGHLY ALLOIMMUNIZED KIDNEY TRANSPLANT CANDIDATE
EHA Library, Jens Schrezenmeier, 4159560
PRECLINICAL MODELLING AND MECHANISTIC INSIGHTS INTO CAR-T CELL INDUCED NEUROTOXICITY
EHA Library, Rita El Khoury, 4159561
MULTI-OMIC ANALYSIS OF GUT MICROENVIRONMENT IN CHIMERIC ANTIGEN RECEPTOR T CELL-TREATED SYNERGETIC MICE FINDING PARVIBACTOR AS CRITICAL MICROBIOTA FOR ACTIVATING ENDOGENOUS CD8+ T CELLS
EHA Library, Kejia Hu, 4159562
BASE EDITING FOR SICKLE CELL DISEASE: ONGOING RESULTS FROM THE BEACON STUDY EVALUATING THE SAFETY AND EFFICACY OF BEAM-101, THE FIRST BASE-EDITED AUTOLOGOUS CD34+ HSPC ONE-TIME CELL THERAPY
EHA Library, Ashish Gupta, 4159563
RAPCABTAGENE AUTOLEUCEL (YTB323) IN PATIENTS WITH RELAPSED/REFRACTORY DIFFUSE LARGE B-CELL LYMPHOMA: A PHASE II TRIAL CLINICAL UPDATE
EHA Library, Mi Kwon, 4159564
INTRA-CSF DELIVERY OF DUAL CD19/CD22 CAR-T THERAPY FOR RELAPSED/REFRACTORY CENTRAL NERVOUS SYSTEM B-CELL MALIGNANCIES: FIRST-IN-HUMAN CLINICAL TRIAL
EHA Library, Qingming Wang, 4159565
IMMUNE CELL SUBSETS AND CYTOKINE PROFILES ARE ASSOCIATED WITH IMMUNE-RELATED HYPERINFLAMMATORY STATES AFTER CAR T-CELL THERAPY
EHA Library, Melinda Tan, 4159566
RED BLOOD CELL (RBC) HEALTH AND FUNCTION POST BEAM-101 TREATMENT: MULTIPLE EXPLORATORY BIOMARKERS DEMONSTRATE RHEOLOGY AND SICKLING PARAMETERS COMPARABLE TO SICKLE CELL TRAIT (SCT)
EHA Library, Priya S. Chockalingam, 4159567
DURABLE CLINICAL BENEFITS AND IMPROVEMENT OF TISSUE IRON OVERLOAD WITH EXAGAMGLOGENE AUTOTEMCEL FOR TRANSFUSION-DEPENDENT THALASSEMIA
EHA Library, Franco Locatelli, 4159568
CD19/CD22 BISPECIFIC CAR-T CELL THERAPY FOR RELAPSED/REFRACTORY LARGE B-CELL LYMPHOMA: A PROSPECTIVE, SINGLE-ARM, SINGLE-CENTER, PHASE 2 CLINICAL TRIAL
EHA Library, Liang Wang, 4159569
DURABLE CLINICAL BENEFITS WITH EXAGAMGLOGENE AUTOTEMCEL FOR SICKLE CELL DISEASE WITH RECURRENT VASO-OCCLUSIVE CRISIS AND FACTORS IMPACTING CD34+ HEMATOPOIETIC STEM CELL COLLECTION
EHA Library, Haydar Frangoul, 4159570
BCMA+ PLASMA CELLS CONTRIBUTE TO RELAPSE AFTER CD19 CAR T-CELL THERAPY IN MULTI-REFRACTORY AUTOIMMUNE HEMOLYTIC ANEMIA
EHA Library, Ruonan Li, 4159571
DENDRITIC CELL-BASED VACCINES (KSD-101) AGAINST EBV-ASSOCIATED LYMPHOPROLIFERATIVE DISEASES: RESULTS FROM AN ONGOING PHASE I CLINICAL STUDY
EHA Library, chunrui li, 4159572
INOTUZUMAB-BASED PROTOCOLS ARE SAFE AND EFFECTIVE IN PATIENTS WITH RELAPSED/REFRACTORY B-ACUTE LYMPHOBLASTIC LEUKEMIA PLANNED FOR CD19 CAR-T CELL THERAPY.
EHA Library, Anupa John, 4159573
AUTOLOGOUS AND DONOR-DERIVED CD7-KNOCKOUT CD7-TARGETED CAR T THERAPY IN RELAPSED OR REFRACTORY T-CELL ACUTE LYMPHOBLASTIC LEUKEMIA: A PHASE 1/2 CLINICAL STUDY
EHA Library, Jing Pan, 4159574
UNCOVERING CAR-T THERAPY EFFICACY AND TOXICITY THROUGH CELL-FREE DNA PROFILING
EHA Library, Daniela Cesana, 4159575
A PHASE I STUDY OF GPRC5D TARGETING CAR T-CELL THERAPY CT071 FOR HIGH-RISK NEWLY DIAGNOSED MULTIPLE MYELOMA
EHA Library, Juan Du, 4159576
Integrated Editing and Manufacturing Process Design for BEAM-101, an Autologous CD34+ HSPC Therapy for Sickle Cell Disease, Results in Robust Process Yield and Increased HbF Induction
EHA Library, Paul Kopesky, 4159577
CD123-SPECIFIC CAR-T CELLS PRODUCED BY LINEAR DNA-BASED PIGGYBAC TRANSPOSON SYSTEM - INITIATION OF PHASE I CLINICAL TRIAL IN PATIENTS WITH AML
EHA Library, Pavel Otáhal, 4159578
SAFETY AND EFFICACY OF POLATUZUMAB VEDOTIN PLUS GLOFITAMAB AS BRIDGING THERAPY PRIOR TO TALICABTAGENE AUTOLEUCEL FOR RELAPSED/ REFRACTORY B-CELL LYMPHOMA
EHA Library, Thomas Eipe, 4159579
COST-EFFECTIVENESS OF REAL-WORLD AXICABTAGENE CILOLEUCEL USE IN RELAPSED/REFRACTORY 2L LBCL BASED ON A MULTI-CENTER US REGISTRY
EHA Library, Olalekan Oluwole, 4159580
NEUROPATHIC CHRONIC PAIN IN SICKLE CELL DISEASE IS ASSOCIATED WITH WORSE QUALITY OF LIFE, HEMOLYSIS, AND TNF INFLAMMATION
EHA Library, Angela Liu, 4159581
PHARMACOKINETICS (PK), PHARMACODYNAMICS (PD), AND SAFETY OF THE NOVEL ORAL FETAL HEMOGLOBIN (HBF) INDUCER POCIREDIR IN HEALTHY ADULTS IN A PHASE 1 STUDY
EHA Library, Caterina Minniti, 4159582
LEFT VENTRICULAR STRAIN IN PEDIATRIC SICKLE CELL DISEASE: INSIGHTS INTO SUBCLINICAL MYOCARDIAL DYSFUNCTION
EHA Library, Miguel R. Abboud, 4159583
PREGNANCIES IN SICKLE CELL PATIENTS IN AN AREA OF HIGH SOCIO-ECONOMIC DEPRIVATION REVEAL HIGH LEVELS OF MATERNAL AND FETAL COMPLICATIONS
EHA Library, Louise Caldwell, 4159584
PEOPLE WITH SICKLE CELL DISEASE EXPERIENCE SUBSTANTIAL SYMPTOM IMPACT DESPITE TREATMENT: FINDINGS FROM THE GLOBAL LISTEN SURVEY
EHA Library, Raffaella Colombatti, 4159585
IDENTIFYING POTENTIAL BIOMARKERS OF CLINICAL RELEVANCE IN SICKLE CELL TRAIT: INTERIM FINDINGS FROM THE NATIONAL ALLIANCE OF SICKLE CELL CENTERS AUNT STUDY
EHA Library, Julie Kanter, 4159586
SICKLE CELL DISEASE AND IRON
EHA Library, Simone Villaboni, 4159587
OPTIMIZING HYDROXYUREA THERAPY IN SICKLE CELL DISEASE: INSIGHTS FROM METABOLITE DETECTION, TREATMENT RESPONSE AND CLINICAL OUTCOMES
EHA Library, Sigrid van der Veen, 4159588
A COMPREHENSIVE LONGITUDINAL STUDY FOR MULTIPLE ORGAN DAMAGE IN A COHORT OF INDIAN SICKLE CELL DISEASE- A TWO YEARS FOLLOW-UP STUDY.
EHA Library, Nikhil Shinde, 4159589
MITOCHONDRIAL RETENTION IN SICKLE CELL DISEASE: CONNECTING RED BLOOD CELL BIOLOGY TO DISEASE HETEROGENEITY
EHA Library, Alkmini Anastasiadi, 4159590
OXIDATIVE METABOLISM IMPROVEMENT DURING EXERCISE IN SICKLE CELL DISEASE PATIENTS TREATED 12 MONTHS WITH VOXELOTOR. ANALYSIS OF HEMOPROVE TRIAL.
EHA Library, Thomas d'Humières, 4159591
THE EFFECT OF SPECIALISED PRO-RESOLVING MEDIATORS ON HAEMATOPOIETIC STEM CELL IMPRINTING AND NEUTROPHIL ACTIVATION IN SICKLE CELL DISEASE
EHA Library, Vishaka Gorur, 4159592
TRANSFUSION AFTER PROPHYLACTIC ECULIZUMAB USE IN INDIVIDUALS WITH SICKLE CELL DISEASE AND A HISTORY OF DELAYED HEMOLYTIC TRANSFUSION REACTION: A SINGLE-CENTER CASE SERIES
EHA Library, Brittany McCrary, 4159593
UNDERSTANDING THE BURDEN OF ILLNESS IN A COHORT OF INDIAN SICKLE CELL DISEASE PATIENTS.
EHA Library, Nikhil Shinde, 4159594
PRELIMINARY VALIDATION OF THE DYNAMIC SICKLING ASSAY (DSA) AS A DIAGNOSTIC TOOL FOR ASSESSING SICKLE CELL DISEASE SEVERITY AND MONITORING THERAPY EFFICACY
EHA Library, Patrick Hines, 4159595
SAFETY AND EFFICACY OF ADDITION OF FILGRASTIM TO CD34+ CELL HARVESTING IN FOUR CASES OF SICKLE CELL DISEASE PATIENTS FOR GENOME EDITING
EHA Library, Francesco Arcioni, 4159596
ENHANCING CARE FOR SICKLE CELL PATIENTS WITH A REAL-TIME LONGITUDINAL PATIENT TRACKING FACILITY WITHIN AN ELECTRONIC PATIENT RECORD SYSTEM
EHA Library, Portia Smith, 4159597
COMPUTATIONAL ANALYSIS OF IMMUNOPHENOTYPIC PERTURBATIONS OF PERIPHERAL BLOOD MONONUCLEAR CELLS IN SICKLE CELL DISEASE
EHA Library, Elisabeth Dovern, 4159598
THE IMPACT OF LUSPATERCEPT ON ERYTHROPOIESIS IN A REAL-WORLD COHORT OF TRANSFUSION-DEPENDENT ß-THALASSEMIA PATIENTS
EHA Library, Valentina BRANCALEONI, 4159599
F-BMT CONDITIONING REGIMEN IMPROVES THE EFFICACY AND SAFETY OF ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR TRANSFUSION-DEPENDENT THALASSEMIA: A SINGLE-ARM CLINICAL TRIAL
EHA Library, Xiaolin Yin, 4159600
DEVELOPING DRUGGABLE GENE EDITING TOOLS FOR ß-THALASSEMIA: TARGETED MODULATION OF BCL11A ZINC FINGER DOMAINS
EHA Library, Afsar Ali Mian, 4159601
EVALUATION OF ATHEROSCLEROSIS AND ATHEROSCLEROSIS RISK FACTORS IN AN AGING COHORT OF BETA THALASSEMIA PATIENTS.
EHA Library, Natalia Scaramellini, 4159602
ASSESSMENT OF SERUM NEUTROPHIL GELATINASE-ASSOCIATED LIPOCALIN (NGAL) LEVELS IN PATIENTS WITH TRANSFUSION DEPENDENT ß-THALASSEMIA (TDT)
EHA Library, Elena CHATZIKALIL, 4159603

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