MANAGEMENT OF IMMUNE EFFECTOR CELL-ASSOCIATED NEUROTOXICITY SYNDROME FOLLOWING CAR-T CELL THERAPY IN CLINICAL PRACTICE: A MULTICENTRIC, RETROSPECTIVE, REAL-WORLD ANALYSIS OF TREATMENT APPROACHES AND OUTCOMES
EHA Library, Veit Bücklein,
4161223
POCIREDIR, A POTENT AND SELECTIVE EED INHIBITOR FOR THE TREATMENT OF SICKLE CELL DISEASE, INDUCES TARGET ENGAGEMENT AND GENE EXPRESSION CHANGES THAT ARE SPECIFIC AND REVERSIBLE IN WILD-TYPE MICE
EHA Library, Caterina Minniti,
4161249
PATIENT-REPORTED VASO-OCCLUSIVE EVENTS, THEIR ASSOCIATED PAIN SEVERITY, AND IMPACT OF SICKLE CELL DISEASE ON FATIGUE AND QUALITY OF LIFE: A REAL-WORLD SURVEY IN THE UNITED STATES
EHA Library, Oladipo Cole,
4161253
UPDATED SAFETY AND EFFICACY RESULTS OF RM-001, AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS, IN TREATING TRANSFUSION-DEPENDENT ß-THALASSEMIA
EHA Library, Hui Xu,
4161255
SINGLE- AND MULTIPLE-ASCENDING DOSES OF DISC-3405, A RECOMBINANT HUMANIZED ANTIBODY TARGETING TMPRSS6, INCREASED HEPCIDIN AND REDUCED IRON AND HEMATOCRIT IN HEALTHY VOLUNTEERS
EHA Library, Marcus Carden,
4161281
EFFECTIVENESS AND SAFETY OF AVATROMBOPAG FOR THE TREATMENT OF ADULTS WITH NEWLY DIAGNOSED, PERSISTENT, OR CHRONIC IMMUNE THROMBOCYTOPENIA: INTERIM RESULTS FROM THE PHASE 4 ADOPT STUDY
EHA Library, Waleed Ghanima,
4161305
EFFICACY AND SAFETY OF AVATROMBOPAG FOR THE TREATMENT OF PEDIATRIC IMMUNE THROMBOCYTOPENIA IN THE OPEN-LABEL EXTENSION OF A PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED TRIAL
EHA Library, Rachael F. Grace,
4161308
CLINICAL FACTORS ASSOCIATED WITH RESPONSE TO RILZABRUTINIB, A BRUTON TYROSINE KINASE (BTK) INHIBITOR, IN PATIENTS WITH IMMUNE THROMBOCYTOPENIA (ITP) TREATED IN THE PHASE 3 LUNA3 STUDY
EHA Library, David Kuter,
4161314