RISK OF SERIOUS INFECTIONS IN PATIENTS WITH OR WITHOUT PAROXYSMAL NOCTURNAL HEMOGLOBINURIA: A REAL-WORLD MATCHED COHORT ANALYSIS
EHA Library, Richard Ofori-Asenso, 325356
REAL WORLD DATA OF PATIENTS WITH ACQUIRED PURE RED CELL APLASIA: A SINGLE INSTITUTION EXPERIENCE
EHA Library, Moon Ley Tung, 325357
CLINICAL CHARACTERISTICS OF 512 ECULIZUMAB-NAIVE PAROXYSMAL NOCTURNAL HEMOGLOBINURIA PATIENTS IN CHINA: A SINGLE-CENTER OBSERVATIONAL STUDY
EHA Library, Yali Du, 325358
IMPACT OF UNFAVORABLE GENETICS ON MINIMAL RESIDUAL DISEASE (MRD) RESPONSE TO VENETOCLAX+RITUXIMAB RETREATMENT IN RELAPSED OR REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA (R/R CLL): PHASE 3 MURANO SUBSTUDY
EHA Library, Jenny Qun Wu, 325359
TPL2 ABLATION ACCELERATES DISEASE DEVELOPMENT IN CHRONIC LYMPHOCYTIC LEUKEMIA EU-TCL1 MOUSE MODEL
EHA Library, Jessica Bordini, 325360
LONG NON‐CODING RNA LINC00525 PROMOTES PROLIFERATION AND INHIBITS APOPTOSIS OF CHRONIC LYMPHOCYTIC LEUKEMIA CELLS BY TARGETING MIR‐338‐3P/WWP1 AXIS
EHA Library, Lei Fan, 325361
COMPARING MACHINE LEARNING-BASED PREDICTION OF TREATMENT IN CLL USING RECURRENT GENE MUTATIONS VERSUS (PARA)CLINICAL FEATURES
EHA Library, Mehdi Parviz, 325362
MULTIREGIONAL SEQUENCING AND CIRCULATING TUMOR DNA ANALYSIS PROVIDE COMPLEMENTARY APPROACHES FOR COMPREHENSIVE DISEASE PROFILING OF SMALL LYMPHOCYTIC LYMPHOMA
EHA Library, Riccardo Moia, 325363
CFOS/MIR-181A CIRCUITRY IS INVOLVED IN BCR SIGNALLING AND DEATH OF CLL CELLS.
EHA Library, Alice Ramassone, 325364
NUSAP1 ENHANCES DRUG RESISTANCE BY BINDING TO RAD51 THROUGH DNA DAMAGE REPAIR PATHWAY IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Yang Han, 325365
CLINICAL VALIDATION OF A NGS CAPTURE PANEL TO IDENTIFY MUTATIONS, COPY NUMBER ALTERATIONS AND CHROMOSOMAL REARRANGEMENTS IN MATURE B-CELL NEOPLASMS
EHA Library, Andrea Gomez Llonin, 325366
INFLUENCE OF THE STATE OF THE 'TELOMERE-TELOMERASE' SYSTEM ON THE COURSE OF CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Isaeva Natalia, 325367
BCMA AS A TARGET FOR T-CELL REDIRECTING BISPECIFIC ANTIBODIES IN B-CELL LYMPHOMAS AND CLL
EHA Library, Anne Martens, 325368
IN SILICO PREDICTION REVEALS PUTATIVE T-CELL CLASS I NEOEPITOPES WITHIN THE CLONOTYPIC BCR IG OF CLL PATIENTS
EHA Library, Anna Vardi, 325369
SWATH-MS PROTEOMICS AS A NEW TOOL FOR DISCOVERING POTENTIAL DRUG TARGETS AND BIOMARKERS IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Umair T Khan, 325370
CHARACTERIZATION OF STAT5B MUTATIONS AND TCRΒ REPERTOIRE IN CD4+ T LARGE GRANULAR LYMPHOCYTE LEUKEMIA
EHA Library, Antonella Teramo, 325371
AUTOPHAGY-RELATED GENETIC VARIANTS INFLUENCE THE RISK OF DEVELOPING CHRONIC LYMPHOCYTIC LEUKEMIA: A STUDY IN THE CONTEXT OF THE CRUCIAL CONSORTIUM
EHA Library, Ana Moñiz Díez, 325372
THE GUT MICROBIOME IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Tereza Faitova, 325373
EX VIVO DRUG SENSITIVITY IDENTIFIES COMBINATION TREATMENT WITH PI3K/BCL-2 INHIBITORS FOR MONOTHERAPY-REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Sigrid Skånland, 325374
THE IGLV3-21 LIGHT CHAIN ANALYSIS IN CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Nadiia Bilous, 325375
ANALYSIS OF GENOMIC COMPLEXITY IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) USING OPTICAL GENOME MAPPING
EHA Library, Anna Puiggros, 325376
THE IDO-KYN-AHR PATHWAY PROMOTES CHRONIC LYMPHOCYTIC LEUKEMIA CELLS SURVIVAL AND MITIGATES THE APOPTOTIC EFFECT OF ABT-199
EHA Library, Claudio Giacinto Atene, 325377
LNCRNA LANDSCAPE ANALYSIS IDENTIFIED LNCRNA LEF-AS1 AS AN ONCOGENE THAT UPREGULATES LEF1 AND PROMOTES SURVIVAL IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Lei Fan, 325378
DISCOVERY OF HBW-3-10: A POTENT, ORALLY ACTIVE, REVERSIBLE BRUTON’S TYROSINE KINASE (BTK) INHIBITOR WITH ANTITUMOR ACTIVITIES IN MICE
EHA Library, Chester Yuan, 325379
TARGETING CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) CELLS WITH THE GLYCOGEN SYNTHASE KINASE-3 BETA (GSK-3Β)-SELECTIVE SMALL MOLECULE INHIBITOR, 9-ING-41
EHA Library, Estevao Carlos Silva Barcelos, 325380
INFLUENCE OF POLYMORPHISMS OF CODON 72 OF TP53 IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Martin-Antonio Cabero-Becerra, 325381
CRISPR/CAS9 AND MRNA-BASED GENE EDITING AND EXPRESSION IN CHRONIC LYMPHOCYTIC LEUKEMIA CELLS
EHA Library, Anna Kabanova, 325382
THE SIGNS OF NEGATIVE SELECTION IN IGHV FRAMEWORK REGIONS ARE ASSOCIATED WITH WORSE OVERALL SURVIVAL OF CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Iryna Abramenko, 325383
GENE EXPRESSION MODEL TO IDENTIFY CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) PATIENTS WITH AN ULTRA-STABLE DISEASE. A CAMPUS CLL STUDY.
EHA Library, Ilaria Del Giudice, 325384
SOMATIC HYPERMUTATION PROFILES IN STEREOTYPED IGHV4-34 RECEPTORS FROM SOUTH AMERICAN CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Carmen Stanganelli, 325385
NGS APPROACH FOR IGHV REARRANGEMENT ANALYSIS IN CLL PATIENTS WITH OLIGOCLONAL DISEASE
EHA Library, Bella Biderman, 325386
SYSTEMATIC TRANSCRIPTOME ANALYSIS REVEALS DISTINCT COMPETING ENDOGENOUS RNA NETWORK IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Ya Zhang, 325387
CHRONIC LYMPHOCYTIC LEUKAEMIA (CLL): HIGH-RISK DATA FROM AN IRISH POPULATION.
EHA Library, Carmel Waldron, 325388
INFLUENCE OF INFLAMMATORY CYTOKINES ON S100A PROTEINS EXPRESSION IN CLL PATIENTS
EHA Library, Olivera Mitrovic, 325389
RELEVANCE OF NRF2/KEAP1 AXIS IN CHRONIC LYMPHOCYTIC LEUKEMIA DEVELOPMENT
EHA Library, Ana Bela Sarmento-Ribeiro, 325390
OTHER MALIGNANCIES IN THE HISTORY OF CHRONIC LYMPHOCYTIC LEUKEMIA – A RETROSPECTIVE, MULTICENTER COHORT STUDY BY ERIC, THE EUROPEAN RESEARCH INITIATIVE ON CLL, IN HARMONY
EHA Library, Thomas Chatzikonstantinou, 325391
VENETOCLAX-OBINUTUZUMAB MODULATES CLONAL GROWTH: RESULTS OF A POPULATION-BASED MINIMAL RESIDUAL DISEASE MODEL FROM THE RANDOMIZED CLL14 STUDY
EHA Library, Othman Al-Sawaf, 325392
PIRTOBRUTINIB (LOXO-305), A NEXT GENERATION, HIGHLY SELECTIVE, NON-COVALENT BTK INHIBITOR IN PREVIOUSLY TREATED CLL/SLL: RESULTS FROM THE PHASE 1/2 BRUIN STUDY
EHA Library, Lindsey Roeker, 325393
MINIMAL RESIDUAL DISEASE-DRIVEN TREATMENT INTENSIFICATION WITH SEQUENTIAL ADDITION OF IBRUTINIB (IBR) TO VENETOCLAX (VEN) IN RELAPSED/REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA (CLL): THE IMPROVE STUDY
EHA Library, Lydia Scarfò, 325394
REAL-WORLD APPLICATION OF NATIONAL COMPREHENSIVE CANCER NETWORK CLINICAL PRACTICE GUIDELINES IN ONCOLOGY (NCCN GUIDELINES®) FOR CLL/SLL FROM THE INFORMCLL REGISTRY
EHA Library, Jacqueline Barrientos, 325395
IBRUTINIB TREATMENT IN THE FIRST-LINE SETTING FOR PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: UP TO 7 YEARS OF FOLLOW-UP IN THE RESONATE-2 STUDY
EHA Library, Paolo Ghia, 325396
SECOND PRIMARY MALIGNANCIES IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: A NATIONWIDE, POPULATION-BASED STUDY IN THE NETHERLANDS
EHA Library, Lina Van Der Straten, 325397
TG-1701, A SELECTIVE BRUTON TYROSINE KINASE (BTK) INHIBITOR, AS MONOTHERAPY AND IN COMBINATION WITH UBLITUXIMAB AND UMBRALISIB (U2) IN CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) AND LYMPHOMA
EHA Library, Chan Cheah, 325398
ZANUBRUTINIB MONOTHERAPY IN PATIENTS WITH RELAPSED OR REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA: 34-MONTH FOLLOW-UP RESULTS
EHA Library, Wei Xu, 325399
CONDITIONAL RELATIVE SURVIVAL AMONG PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: A NATIONWIDE, POPULATION-BASED STUDY IN THE NETHERLANDS
EHA Library, Lina Van Der Straten, 325400
SYSTOLIC FUNCTION OF THE LEFT VENTRICULAR MYOCARDIAL IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA RECEIVING IBRUTINIB.
EHA Library, Elena Emelina, 325401
PRELIMINARY RESULTS OF THE PHASE 2 STUDY OF ZANUBRUTINIB IN PATIENTS WITH PREVIOUSLY TREATED B-CELL MALIGNANCIES INTOLERANT TO IBRUTINIB AND/OR ACALABRUTINIB
EHA Library, Mazyar Shadman, 325402
A PHASE 1A/B DOSE ESCALATION STUDY OF THE MUTATION AGNOSTIC BTK/FLT3 INHIBITOR LUXEPTINIB (CG-806) IN PATIENTS WITH RELAPSED OR REFRACTORY B-CELL MALIGNANCIES
EHA Library, Rafael Bejar, 325403
TEN-YEAR FOLLOW-UP OF 415 CLL PATIENTS TREATED WITH FLUDARABINE CYCLOPHOSPHAMIDE-BASED CHEMOIMMUNOTHERAPY IN THE FRONTLINE ARCTIC AND ADMIRE TRIALS, A COMPREHENSIVE ASSESSMENT OF PROGNOSTIC FACTORS
EHA Library, David Allsup, 325404
OUTCOME OF 100 TP53-DISRUPTED CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS TREATED FRONT-LINE WITH IBRUTINIB. A REAL-LIFE CAMPUS CLL STUDY.
EHA Library, Andrea Visentin, 325405
REAL-WORLD EFFICACY AND SAFETY OF VENETOCLAX IN CHRONIC LYMPHOCYTIC LEUKAEMIA – FIRST DATA FROM THE VERONE STUDY, IN PATIENTS WITH VENETOCLAX MONOTHERAPY
EHA Library, Loïc Ysebaert, 325406
POTENTIAL CAPABILITIES OF MRNA ROR1 AND MIR-155 FOR MRD ASSESSMENT IN CLL
EHA Library, Marina Stolyar, 325407
SAFETY AND EFFECTIVENESS OF VENETOCLAX IN COMBINATION WITH RITUXIMAB IN ELDERLY PATIENTS WITH RELAPSED/REFRACTORY CLL TREATED UNDER REAL-LIFE CONDITIONS – DATA FROM THE OBSERVATIONAL STUDY VERVE
EHA Library, Ingo Schwaner, 325408
COMPARISON OF VENETOCLAX INPATIENT AND OUTPATIENT RAMP-UP STRATEGIES FOR CLL. UK MULTICENTRE RESTROSPECTIVE STUDY
EHA Library, Rocío Figueroa Mora, 325409
MOLTO, A MULTICENTER, OPEN LABEL, UNCONTROLLED, PHASE II CLINICAL TRIAL ON SAFETY AND EFFICACY OF VENETOCLAX, ATEZOLIZUMAB AND OBINUTUZUMAB IN RICHTER TRANSFORMATION OF CLL: SAFETY INTERIM ANALYSIS
EHA Library, Anna Maria Frustaci, 325410
TREATMENT OF CLL RELAPSED/REFRACTORY PATIENTS IN COVID-19 PANDEMIC: A REAL-LIFE EXPERIENCE WITH VENETOCLAX-RITUXIMAB COMBINATION IN SOUTHERN ITALY.
EHA Library, stefano molica, 325411
LEUKEMIA CUTIS IN CHRONIC LYMPHOCYTIC LEUKEMIA: A RETROSPECTIVE STUDY OF THE FRENCH INNOVATIVE LEUKEMIA ORGANIZATION (FILO)
EHA Library, Gregory Lazarian, 325412
MANAGEMENT OF PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA AND ARTERIAL HYPERTENSION WHO ARE ON IBRUTINIB THERAPY.
EHA Library, Elena Emelina, 325413
EFFECTIVENESS AND SAFETY OF IBRUTINIB IN CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) AND MANTLE CELL LYMPHOMA (MCL) IN BELGIAN ROUTINE CLINICAL PRACTICE WITH A 3-YEAR FOLLOW-UP
EHA Library, Ann Janssens, 325414
NEUTROPHIL EXTRACELLULAR TRAPS ARE INCREASED IN CHRONIC MYELOID LEUKEMIA AND ARE DIFFERENTIALLY AFFECTED BY TYROSINE KINASE INHIBITORS
EHA Library, Alona Telerman, 325415
PROFILES OF NK CELL SUBSETS ARE ASSOCIATED WITH SUCCESSFUL TYROSINE KINASE INHIBITOR DISCONTINUATION IN CHRONIC MYELOID LEUKEMIA AND CHANGE FOLLOWING INTERFERON TREATMENT
EHA Library, Hao Jiang, 325416
TNF-MEDIATED CML CELL SURVIVAL RESISTS TKI TREATMENT AND THIS CAN BE TARGETED BY IKK2-INHIBITION
EHA Library, Marlena Bütow, 325417
AGE-RELATED DNA DAMAGE RESPONSE (DDR) IN HEMATOPOIETIC STEM CELLS FROM CHRONIC MYELOID LEUKAEMIA PATIENTS WHO ATTEMPTED TKI DISCONTINUATION.
EHA Library, Chiara Manfroni, 325418
ASSESSMENT OF LEUKEMIC STEM CELL CD26+ IN CHRONIC MYELOID LEUKEMIA PATIENTS WITH DEEP MOLECULAR RESPONSE.
EHA Library, Raquel Bengió, 325419
EUTOS EXPERIENCE OF STANDARDISATION OF MOLECULAR MONITORING FOR CML (2016 – 2020). USE OF SECONDARY BCR-ABL1 REFERENCE MATERIALS FOR CONVERSION FACTOR VALIDATION AND ASSESSMENT OF MR4.5 DETECTION
EHA Library, Helen White, 325420
ANALYSIS OF MRNA AND DNA LEVEL OF ATYPICAL BCR-ABL1 TRANSCRIPTS IN CML PATIENTS OUTLINED AN ELIGIBILITY FOR TKI STOPPING
EHA Library, Katerina Machova Polakova, 325421
ANALYSIS OF MYELOID MUTATIONS IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA AND THEIR ASSOCIATION WITH ADVERSE EVENTS AND RELAPSE AFTER DISCONTINUATION.
EHA Library, Adrian Segura Diaz, 325422
COMPREHENSIVE IMMUNOPROFILE OF NK CELLS FROM CML PATIENTS IN TFR REVEALS A POSSIBLE ROLE OF MEMORY-LIKE NK CELLS
EHA Library, Maria Belen Sanchez, 325423
TARGETING THE LEUKEMIC STEM CELL NICHE BY PI3K INHIBITORS IN CHRONIC MYELOID LEUKEMIA TO OVERCOME LEUKEMIC STEM CELL RESISTANCE
EHA Library, Yüksel Filik, 325424
RARE MUTATIONS IN BCR-ABL THE KINASE DOMAIN IN CRONIC MYELOID LEUKEMIA PATIENTS.
EHA Library, Rocío Delamer, 325425
NEGATIVE PROGNOSTIC IMPACT OF HIGH-RISK ADDITIONAL CYTOGENETIC ABNORMALITIES IN ADDITION TO THE ELTS IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Camille C.B. Kockerols, 325426
TREATMENT-FREE REMISSION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE FOLLOWING FRONTLINE NILOTINIB: RESULTS FROM JALSG N-STOP216
EHA Library, Naoto Takahashi, 325427
TREATMENT-FREE REMISSION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE FOLLOWING FRONTLINE DASATINIB: RESULTS FROM JALSG D-STOP216
EHA Library, Yosuke Minami, 325428
COMPARISON OF THE SOKAL AND EUTOS LONG-TERM SURVIVAL SCORES IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA RECEIVING TYROSINE KINASE INHIBITORS
EHA Library, Xiaoshuai Zhang, 325429
ASCIMINIB RESPONSES IN PONATINIB-PRETREATED PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Alejandro Luna, 325430
OUTCOMES BEFORE AND AFTER DOSE REDUCTION IN PATIENTS WITH NEWLY DIAGNOSED CHRONIC MYELOID LEUKEMIA RECEIVING BOSUTINIB OR IMATINIB
EHA Library, Michael W Deininger, 325431
SECOND-LINE BOSUTINIB FOR PATIENTS WITH CHRONIC PHASE CHRONIC MYELOID LEUKEMIA : FINAL 10-YEAR RESULTS OF A PHASE 1/2 STUDY
EHA Library, Carlo Gambacorti-Passerini, 325432
TREATMENT-FREE REMISSION IN CHRONIC MYELOID LEUKEMIA PATIENTS TREATED WITH LOW-DOSE TKIS. A FEASIBLE OPTION ALSO IN THE REAL-LIFE SETTING?
EHA Library, Alessandra Iurlo, 325433
COVID-19 IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA: DISEASE OUTCOMES AND FIRST VACCINATION DATA IN RUSSIAN FEDERATION
EHA Library, Ekaterina Chelysheva, 325434
ASSOCIATION OF CREATINE KINASE ELEVATION WITH CLINICAL OUTCOMES IN CHRONIC MYELOID LEUKEMIA
EHA Library, Aniket Bankar, 325435
FRONTLINE TREATMENT APPROACHES FOR CML IN MYELOID BLAST PHASE: A SINGLE-CENTER EXPERIENCE OVER 2 DECADES
EHA Library, Kapil Saxena, 325436
EFFECT OF COMORBIDITIES ON PATIENT RESPONSES WITH FIRST-LINE DASATINIB VERSUS IMATINIB IN CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE: EXPLORATORY POST HOC ANALYSIS OF DASISION
EHA Library, Massimo Breccia, 325437
HYDROXYUREA PRE-TREATMENT IN CHRONIC MYELOID LEUKEMIA PATIENTS: MORE HARM THAN GOOD?
EHA Library, Camille C.B. Kockerols, 325438
FRENCH REAL–LIFE OBSERVATIONAL STUDY 'TOPASE' EVALUATING SAFETY AND EFFICACY OF PONATINIB CONFIRMS INDUCTION OF DEEP MOLECULAR RESPONSES IN 110 RESISTANT OR INTOLERANT CML PATIENTS
EHA Library, Ali Turhan, 325439
WITHDRAWAL SYNDROME AFTER TYROSINE KINASE INHIBITORS DISCONTINUATION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Anna Petrova, 325440
FIRST INTERIM RESULTS OF THE RUSSIAN PROSPECTIVE STUDY OF REDUCTION AND DISCONTINUATION TREATMENT OF TKI (READIT) IN CHRONIC MYELOID LEUKEMIA PATIENTS WITH DEEP MOLECULAR RESPONSE
EHA Library, Margarita Gurianova, 325441
A SURVEY OF HEALTHCARE PROFESSIONALS IN THE UNITED KINGDOM TO DESCRIBE CURRENT PATHWAYS AND MANAGEMENT PRACTICES IN CHRONIC MYELOID LEUKAEMIA: THE ADAPT CML SURVEY
EHA Library, Adam Mead, 325442
TREATMENT ADHERENCE IN CHRONIC MYELOID LEUKEMIA PATIENTS RECEIVING TYROSINE KINASE INHIBITORS
EHA Library, S.M.Amine BENLAZAR, 325443
THE EFFECT OF BODY MASS INDEX ON EFFICACY AND SAFETY OF BOSUTINIB OR IMATINIB IN PATIENTS WITH NEWLY DIAGNOSED CHRONIC MYELOID LEUKEMIA
EHA Library, Tim Brümmendorf, 325444
EFFICACY AND SAFETY RESULTS FROM AN OPEN-LABEL PHASE 2 STUDY OF PARSACLISIB FOR THE TREATMENT OF AUTOIMMUNE HEMOLYTIC ANEMIA (AIHA)
EHA Library, Wilma Barcellini, 325445
RARE ANEMIA DISORDERS EUROPEAN EPIDEMIOLOGICAL PLATFORM (RADEEP): DISTRIBUTION OF PATIENTS AFFECTED BY PYRUVATE KINASE DEFICIENCY IN EUROPE
EHA Library, Maria Del Mar Mañú Pereira, 325446
FOSTAMATINIB FOR THE TREATMENT OF WARM ANTIBODY AUTOIMMUNE HEMOLYTIC ANEMIA (WAIHA): UPDATES FROM THE PHASE 2 AND PHASE 3 CLINICAL TRIALS
EHA Library, Dheepika Weerasinghe, 325447
COMPLEX MODES OF INHERITANCE IN HEREDITARY RED BLOOD CELL DISORDERS: A CASE SERIES STUDY OF 155 PATIENTS
EHA Library, Roberta Russo, 325448
INHIBITION OF COMPLEMENT C1S WITH SUTIMLIMAB IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): 1-YEAR INTERIM RESULTS OF THE PHASE 3 CARDINAL STUDY LONG-TERM FOLLOW-UP
EHA Library, Alexander Röth, 325449
CANCER RISK IN PATIENTS WITH WARM AUTOIMMUNE HAEMOLYTIC ANAEMIA - A NATIONWIDE COHORT STUDY
EHA Library, Stinne Tranekaer, 325450
BASELINE CHARACTERISTICS BY AGE OF A GLOBAL COHORT OF PATIENTS DIAGNOSED WITH PYRUVATE KINASE DEFICIENCY – A DESCRIPTIVE ANALYSIS FROM THE PEAK REGISTRY
EHA Library, Paola Bianchi, 325451
EARLY-ONSET OSTEOPENIA AND OSTEOPOROSIS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY
EHA Library, Hanny Al-Samkari, 325452
PHARMACOLOGIC INHIBITION OF PI3KΔ REDUCES AUTOANTIBODY FORMATION AND IS EFFICACIOUS IN A PRECLINICAL MODEL OF AUTOIMMUNE HEMOLYTIC ANEMIA
EHA Library, Paul Smith, 325453
IMPACT OF OLIPUDASE ALFA ENZYME REPLACEMENT THERAPY ON PULMONARY, VISCERAL AND HEMATOLOGIC MANIFESTATIONS OF ACID SPHINGOMYELINASE DEFICIENCY: 1-YEAR RESULTS OF CLINICAL TRIALS IN CHILDREN AND ADULTS
EHA Library, Maurizio Scarpa, 325454
MITAPIVAT AMELIORATES RED CELL FEATURES AND DECREASES ANEMIA IN BAND 4.2-/- MICE, A MODEL OF HEREDITARY SPHEROCYTOSIS
EHA Library, Alessandro Matte, 325455

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