TARGETING EXHAUSTED CYTOTOXIC T CELLS BY CTLA-4 BLOCKADE PROMOTES ELIMINATION OF NEOPLASTIC CELLS IN HUMAN MYELOFIBROSIS XENOGRAFTS
EHA Library, Lara Tavernari, 419087
THE EFFECT OF METHYLATION ON THE LET-7-BCL-XL-BCL2 AXIS AND THE POTENTIAL USE OF BH3 MIMETIC DRUGS IN HISTIOCYTIC NEOPLASMS
EHA Library, Oshrat Hershkovitz-Rokah, 419088
EFFICACY OF INCA033989 IN CHRONIC AND ADVANCED FORMS OF CALRDEL52 AND CALRINS5 MYELOPROLIFERATIVE NEOPLASMS (MPN) MODELS
EHA Library, Isabelle Plo, 419089
THE ATYPICAL CHEMOKINE RECEPTOR CCRL2 IS UPREGULATED AND PROMOTES INTERFERON-GAMMA SIGNALING IN ADVANCED MYELOPROLIFERATIVE NEOPLASMS.
EHA Library, Theodora Chatzilygeroudi, 419090
UMBILICAL CORD MESENCHYMAL STROMAL CELLS AMELIORATE MYELOFIBROSIS IN VIVO.
EHA Library, Chien-Chin Lin, 419091
TAGRAXOFUSP EXHIBITS ANTITUMORAL ACTIVITY IN PRECLINICAL MODELS OF MYELOFIBROSIS AND ENHANCES ANTILEUKEMIC ACTIVITY OF JAK INHIBITORS
EHA Library, Vittoria Nicolis di Robilant, 419092
ADVANCING EARLY DETECTION AND IMPROVED TARGETED THERAPY IN MYELOPROLIFERATIVE NEOPLASMS: INSIGHTS FROM MULTIMODAL IMAGING AND NANOPARTICLE-MEDIATED DRUG DELIVERY
EHA Library, Julian Baumeister, 419093
SINGLE CELL MULTIOMICS IDENTIFIES ABERRANT COMMUNICATION BETWEEN DENDRITIC CELLS AND LEUKAEMIA STEM CELLS AS A THERAPEUTICALLY TARGETABLE AXIS IN JUVENILE MYELOMONOCYTIC LEUKAEMIA
EHA Library, Eleni Louka, 419094
TARGETED T CELLS AGAINST HEMATOPOIETIC CELLS EXPRESSING ONCOGENIC CALRETICULIN MUTANTS
EHA Library, Robert Kralovics, 419095
TET2 ADDITIONAL MUTATIONS AT DIAGNOSIS IMPACT THE RESPONSE OF FIRST-LINE TREATMENT WITH HYDROXYUREA OR INTERFERON-Α IN ESSENTIAL THROMBOCYTHEMIA
EHA Library, Carole Mosnier, 419096
ESTABLISHMENT OF A NOVEL PRECLINICAL MOUSE MODEL FOR ADVANCED SYSTEMIC MASTOCYTOSIS
EHA Library, Martina Konantz, 419097
IMPACT OF GENETIC BACKGROUND ON THE FIBROTIC TRANSFORMATION IN MURINE MPN-MODELS
EHA Library, Yu-An Lin, 419098
T-cell engaging immunotherapy in early treatment of B-cell acute lymphoblastic leukemia (B-ALL)
EHA Library, Amgen, 4144088
How to Make the Most out of a Rapidly Evolving Treatment Landscape: Bispecific Antibodies in Relapsed Refractory Multiple Myeloma (RRMM)
EHA Library, Pfizer, 4144087
RESULTS FROM THE RANDOMIZED PHASE 3 DREAMM-8 STUDY OF BELANTAMAB MAFODOTIN PLUS POMALIDOMIDE AND DEXAMETHASONE VS POMALIDOMIDE PLUS BORTEZOMIB AND DEXAMETHASONE IN REPALPSED/REFRACTORY MULTIPLE MYELOMA
EHA Library, Meletios Dimopoulos, 4136513
INTRA- AND EXTRACELLULAR PROTEOME DYNAMICS DURING NORMAL AND MALIGNANT HEMATOPOIETIC STEM CELL EXPANSION
EHA Library, Maria Jassinskaja, 4136514
ACALABRUTINIB PLUS BENDAMUSTINE AND RITUXIMAB IN UNTREATED MANTLE CELL LYMPHOMA: RESULTS FROM THE PHASE 3, DOUBLE-BLIND, PLACEBO-CONTROLLED ECHO TRIAL
EHA Library, Michael L. Wang, 4136515
VITAMIN C SUPPLEMENTATION IN PATIENTS WITH CLONAL CYTOPENIA OF UNDETERMINED SIGNIFICANCE OR LOW-RISK MYELOID MALIGNANCIES: RESULTS FROM EVI-2, A RANDOMIZED, PLACEBO-CONTROLLED PHASE 2 STUDY
EHA Library, Stine Ulrik Mikkelsen, 4136519
ELEVATED HEMOGLOBIN OF ANDEAN AYMARAS IS CAUSED BY ALTERNATIVELY SPLICED NFKB1
EHA Library, Josef Prchal, 4136518
ELA026 TARGETING OF SIRP(+) IMMUNE CELLS RESULTS IN A HIGH RESPONSE RATE AND IMPROVED 2-MONTH SURVIVAL OF TREATMENT-NAIVE MALIGNANCY-ASSOCIATED HEMOPHAGOCYTIC LYMPHOHISTIOCYTOSIS IN A PHASE 1 STUDY
EHA Library, Abhishek Maiti, 4136517
GLOFITAMAB PLUS GEMCITABINE AND OXALIPLATIN (GLOFIT-GEMOX) FOR RELAPSED/REFRACTORY (R/R) DIFFUSE LARGE B-CELL LYMPHOMA (DLBCL): RESULTS OF A GLOBAL RANDOMIZED PHASE III TRIAL (STARGLO)
EHA Library, Jeremy Abramson, 4136516
Abstract Book 2024
EHA Library, Faculty / Presenters, 422826
Education Session on Pediatric acute myeloid leukemia (AML)
EHA Library, Faculty / Presenters, 402937
Education Session on Novel therapeutic approaches in acute myeloid leukemia (AML)
EHA Library, Faculty / Presenters, 402936
Education Session on Novel agents in multiple myeloma
EHA Library, Faculty / Presenters, 402933
Education Session on Inherited red blood cell disorders
EHA Library, Faculty / Presenters, 402932
Education Session on Hemochromatosis: From novel classification to treatment guidelines
EHA Library, Faculty / Presenters, 402929
Education Session on Hematopoietic stem cell biology and transplantation
EHA Library, Faculty / Presenters, 402928
Education Session on Genetics across all lymphoid malignancies
EHA Library, Faculty / Presenters, 402927
Education Session on Fetal-neonatal cytopenias: Focus on anemia
EHA Library, Faculty / Presenters, 402926
Education Sessions on Diffuse Large B-cell Lymphoma (DLBCL)
EHA Library, Faculty / Presenters, 402925
Education Session on What is hot in hemophilia?
EHA Library, Faculty / Presenters, 402944
Education Session on What's new in myeloproliferative neoplasms (MPN)?
EHA Library, Faculty / Presenters, 402945
Education Session on Myelodysplastic syndromes (MDS)
EHA Library, Faculty / Presenters, 402946
Education Session on Immunotherapy in indolent lymphomas
EHA Library, Faculty / Presenters, 402950
Education Sessions on CNS-involvement in acute lymphoblastic leukemia (ALL)
EHA Library, Faculty / Presenters, 402769
Education Sessions on Chronic myeloid leukemia (CML)
EHA Library, Faculty / Presenters, 402755
Education Session on Chronic lymphocytic leukemia (CLL)
EHA Library, Faculty / Presenters, 402754
Education session on Acute chest syndrome in sickle cell disease
EHA Library, Faculty / Presenters, 402753
Presidential Session II
EHA Library, Faculty / Presenters, 402752
Presidential Session I & Awards
EHA Library, Faculty / Presenters, 402751
Education Session on Acute acquired thrombosis and hemostasis challenges
EHA Library, Faculty / Presenters, 402750
HIGH COMPLETE RESPONSE RATE WITH TNB-486, A NOVEL CD19XCD3 T-CELL ENGAGER, IN RELAPSED/REFRACTORY FOLLICULAR LYMPHOMA: INTERIM RESULTS FROM AN ONGOING PHASE 1 STUDY
EHA Library, Ryan Jacobs, 387924
IMPLICATIONS OF REGISTRY DATA FOR ACUTE MYELOID LEUKEMIA (AML) TREATMENT AND CARE DURING THE COVID-19 PANDEMIC
EHA Library, Bart Scott, 386418
PHASE 1B OMNIVERSE TRIAL: SAFETY AND TOLERABILITY OF ORAL AZACITIDINE IN COMBINATION WITH VENETOCLAX FOR TREATMENT OF ACUTE MYELOID LEUKEMIA
EHA Library, Shaun Fleming, 386396
SURVIVAL OUTCOMES WITH CPX-351 VS 7+3 BY BASELINE BONE MARROW BLAST PERCENTAGE IN OLDER ADULTS WITH NEWLY DIAGNOSED HIGH-RISK OR SECONDARY ACUTE MYELOID LEUKEMIA: A 5-YEAR FOLLOW-UP STUDY
EHA Library, Jorge Cortes, 386346
CARDIOTOXICITY OF CPX-351 VS 7+3 IN PATIENTS WITH UNTREATED HIGH-RISK ACUTE MYELOID LEUKEMIA
EHA Library, Jorge Cortes, 386345
A REAL-WORLD EVALUATION OF TREATMENT PATTERNS AND OUTCOMES OF ACUTE MYELOID LEUKEMIA INDUCTION THERAPIES IN THE COMMUNITY SETTING
EHA Library, Keri Maher, 386344
A FIRST-IN-HUMAN STUDY OF CD123 NK CELL ENGAGER SAR443579 IN RELAPSED OR REFRACTORY ACUTE MYELOID LEUKEMIA, B-CELL ACUTE LYMPHOBLASTIC LEUKEMIA OR HIGH RISK-MYELODYSPLASIA
EHA Library, Anthony Selwyn Stein, 386323
FIVE-YEAR EFFICACY AND SAFETY OF TAFASITAMAB IN PATIENTS WITH RELAPSED OR REFRACTORY DLBCL: FINAL RESULTS FROM THE PHASE II L-MIND STUDY
EHA Library, Johannes Duell, 385588
SAFETY AND EFFICACY OF ACALABRUTINIB, BENDAMUSTINE, AND RITUXIMAB IN PATIENTS WITH TREATMENT-NAIVE OR RELAPSED/REFRACTORY MANTLE CELL LYMPHOMA: PHASE IB TRIAL
EHA Library, Tycel Phillips, 385544
PIRTOBRUTINIB IN COVALENT BTK-INHIBITOR PRE-TREATED MANTLE CELL LYMPHOMA: UPDATED RESULTS AND SUBGROUP ANALYSIS FROM THE PHASE 1/2 BRUIN STUDY WITH >3 YEARS FOLLOW-UP FROM START OF ENROLLMENT
EHA Library, Wojciech Jurczak, 385537
INDIRECT TREATMENT COMPARISON OF MOMELOTINIB VS FEDRATINIB SAFETY IN PATIENTS WITH MYELOFIBROSIS
EHA Library, Francesca Palandri, 385512
LONG-TERM SAFETY WITH ≥12 MONTHS OF PIRTOBRUTINIB IN RELAPSED/REFRACTORY (R/R) B-CELL MALIGNANCIES
EHA Library, Wojciech Jurczak, 386447
A PHASE 3, OPEN-LABEL, RANDOMIZED STUDY EVALUATING THE EFFICACY AND SAFETY OF SINGLE AGENT BELANTAMAB MAFODOTIN VS POMALIDOMIDE PLUS DEXAMETHASONE IN RELAPSED/REFRACTORY MULTIPLE MYELOMA (DREAMM-3)
EHA Library, Meletios Dimopoulos, 387899
LUSPATERCEPT RESTORES EFFECTIVE ERYTHROPOIESIS AND PROVIDES SUPERIOR AND SUSTAINED CLINICAL BENEFIT VS EPOETIN ALFA: BIOMARKER ANALYSIS FROM THE PHASE 3 COMMANDS STUDY
EHA Library, Uwe Platzbecker, 386522
TREATMENT PATTERNS AND OUTCOMES AMONG PATIENTS WITH LOWER-RISK MYELODYSPLASTIC SYNDROMES RECEIVING LUSPATERCEPT IN ROUTINE CLINICAL PRACTICE IN THE UNITED STATES
EHA Library, Sudipto Mukherjee, 386562
BASELINE AND EARLY POST-INFUSION BIOMARKERS ASSOCIATED WITH OPTIMAL RESPONSE TO IDECABTAGENE VICLEUCEL (IDE-CEL) IN THE KARMMA-3 STUDY OF TRIPLE-CLASS–EXPOSED RELAPSED AND REFRACTORY MULTIPLE MYELOMA
EHA Library, Marc S. Raab, 386630
PATIENT REPORTED OUTCOMES IN TRIPLE CLASS EXPOSED, RELAPSED/REFRACTORY MULTIPLE MYELOMA (TCE RRMM) PATIENTS IN KARMMA 3 TRIAL (PHASE 3 RCT):  IDECABTAGENE VICLEUCEL (IDE-CEL) VERSUS STANDARD REGIMENS
EHA Library, Michel Delforge, 386734
PELABRESIB (CPI-0610) MONOTHERAPY IN PATIENTS WITH HIGH-RISK ESSENTIAL THROMBOCYTHEMIA REFRACTORY OR INTOLERANT TO HYDROXYUREA: PRELIMINARY RESULTS FROM MANIFEST STUDY
EHA Library, Francesco Passamonti, 387868
EFFICACY AND SAFETY OF LUSPATERCEPT FOR THE TREATMENT OF ANEMIA IN PATIENTS WITH MYELOFIBROSIS: RESULTS FROM THE ACE-536-MF-001 STUDY
EHA Library, Francesco Passamonti, 387867
LUSPATERCEPT VERSUS EPOETIN ALFA FOR TREATMENT (TX) OF ANEMIA IN ESA-NAIVE LOWER-RISK MYELODYSPLASTIC SYNDROMES (LR-MDS) PATIENTS (PTS) REQUIRING RBC TRANSFUSIONS: DATA FROM THE PHASE 3 COMMANDS STUDY
EHA Library, Matteo Giovanni Della Porta, 387802
FIVE-YEAR SUBGROUP ANALYSIS OF TAFASITAMAB + LENALIDOMIDE FROM THE PHASE II L-MIND STUDY IN PATIENTS WITH RELAPSED OR REFRACTORY DIFFUSE LARGE B-CELL LYMPHOMA
EHA Library, Johannes Duell, 387406
IMPACT OF TRANSFUSION BURDEN ON HEALTH-RELATED QUALITY OF LIFE AND FUNCTIONING IN PATIENTS WITH MYELOFIBROSIS: POST HOC ANALYSIS OF SIMPLIFY-1 AND -2
EHA Library, Ruben Mesa, 387290
EXCALIBER-RRMM: A PHASE 3, TWO-STAGE STUDY OF IBERDOMIDE, DARATUMUMAB, AND DEXAMETHASONE VERSUS DARATUMUMAB, BORTEZOMIB, AND DEXAMETHASONE IN PATIENTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA
EHA Library, Sagar Lonial, 387240
BELANTAMAB MAFODOTIN FOR RELAPSED/REFRACTORY MULTIPLE MYELOMA: A REAL-WORLD OBSERVATIONAL STUDY UPDATE
EHA Library, Michel Delforge, 387224
CLINICAL OUTCOMES BY SF3B1 MUTATION STATUS IN PATIENTS WITH LOWER-RISK MYELODYSPLASTIC SYNDROMES RETREATED WITH ERYTHROPOIESIS-STIMULATING AGENTS
EHA Library, Guillermo Garcia-Manero, 387135
A PHASE 2/3 TRIAL OF ORAL AZACITIDINE IN PATIENTS WITH LOW- OR INTERMEDIATE-RISK MYELODYSPLASTIC SYNDROMES
EHA Library, Guillermo Garcia-Manero, 387132
PATIENT (PT)-REPORTED OUTCOMES IN PTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM) TREATED WITH BELANTAMAB MAFODOTIN (BELAMAF) VS POMALIDOMIDE/LOW DOSE DEXAMETHASONE (PD) IN THE DREAMM-3 STUDY
EHA Library, Vania Hungria, 386793
BASELINE CHARACTERISTICS IDENTIFYING PATIENTS WITH MULTIPLE MYELOMA TREATED WITH IDECABTAGENE VICELEUCEL (IDE-CEL; BB2121) WHO ARE AT RISK FOR SEVERE/REFRACTORY INFLAMMATORY ADVERSE EVENTS
EHA Library, Yi Lin, 386638
LONG-TERM OUTCOMES WITH ISATUXIMAB-CARFILZOMIB-DEXAMETHASONE (ISA-KD) IN RELAPSED MULTIPLE MYELOMA PATIENTS WITH 1Q21+ STATUS: UPDATED RESULTS FROM THE PHASE 3 IKEMA STUDY
EHA Library, Thierry Facon, 386745
A PHASE 1 STUDY OF BELANTAMAB MAFODOTIN IN COMBINATION WITH STANDARD OF CARE IN NEWLY DIAGNOSED MULTIPLE MYELOMA: AN INTERIM ANALYSIS OF DREAMM-9
EHA Library, Saad Z. Usmani, 386693
RESULTS OF A PHASE 3 TRIAL OF AN ORAL CXCR4 ANTAGONIST, MAVORIXAFOR, FOR TREATMENT OF PATIENTS WITH WHIM SYNDROME
EHA Library, Jean Donadieu, 387880
SPLEEN VOLUME REDUCTION PREDICTS SURVIVAL IN MYELOFIBROSIS PATIENTS ON PACRITINIB BUT NOT BEST AVAILABLE THERAPY: PERSIST-2 LANDMARK OVERALL SURVIVAL ANALYSIS
EHA Library, Jan Bewersdorf, 385480
CARTITUDE-1 FINAL RESULTS: PHASE 1B/2 STUDY OF CILTACABTAGENE AUTOLEUCEL IN HEAVILY PRETREATED PATIENTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA
EHA Library, Nikhil Munshi, 387902
TALQUETAMAB (TAL) + DARATUMUMAB (DARA) IN PATIENTS (PTS) WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM): UPDATED TRIMM-2 RESULTS
EHA Library, Nizar J Bahlis, 387892
PIVOTAL PHASE 2 MONUMENTAL-1 RESULTS OF TALQUETAMAB (TAL), A GPRC5DXCD3 BISPECIFIC ANTIBODY (BSAB), FOR RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM)
EHA Library, Cyrille Touzeau, 387891
FIRST RESULTS FROM THE REDIRECTT-1 STUDY WITH TECLISTAMAB (TEC) + TALQUETAMAB (TAL) SIMULTANEOUSLY TARGETING BCMA AND GPRC5D IN PATIENTS (PTS) WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM)
EHA Library, María-Victoria Mateos, 387890
PATIENT PERSPECTIVES ON BCMA-TARGETED THERAPIES FOR MULTIPLE MYELOMA: A SURVEY CONDUCTED IN A PATIENT ADVOCACY GROUP
EHA Library, Jay R. Hydren, 386761
EVALUATION OF PROPHYLACTIC TOCILIZUMAB (TOCI) FOR THE REDUCTION OF CYTOKINE RELEASE SYNDROME (CRS) TO INFORM THE MANAGEMENT OF PATIENTS (PTS) TREATED WITH TECLISTAMAB IN MAJESTEC-1
EHA Library, Niels W C J van de Donk, 386740
ANALYSIS OF INFECTIONS AND PARAMETERS OF HUMORAL IMMUNITY IN PATIENTS (PTS) WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM) TREATED WITH TALQUETAMAB (TAL) MONOTHERAPY IN MONUMENTAL-1
EHA Library, Leo Rasche, 386721
DURABILITY OF RESPONSES WITH BIWEEKLY DOSING OF TECLISTAMAB IN PATIENTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA ACHIEVING A CLINICAL RESPONSE IN THE MAJESTEC-1 STUDY
EHA Library, Manisha Bhutani, 386710
LONG-TERM FOLLOW-UP FROM MAJESTEC-1 OF TECLISTAMAB, A B-CELL MATURATION ANTIGEN (BCMA) X CD3 BISPECIFIC ANTIBODY, IN PATIENTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA (RRMM)
EHA Library, Surbhi Sidana, 386708
LONG-TERM REMISSION AND SURVIVAL IN PATIENTS WITH RELAPSED OR REFRACTORY MULTIPLE MYELOMA AFTER TREATMENT OF LCAR-B38M CAR-T – AT LEAST 5-YEAR FOLLOW-UP IN LEGEND-2
EHA Library, Jian‑Qing Mi, 386703
CONSISTENCY OF PACRITINIB FOR SPLEEN AND SYMPTOM REDUCTION IN PATIENTS WITH MYELOFIBROSIS REGARDLESS OF CYTOPENIAS
EHA Library, Nico Gagelmann, 385487
Abstract Book 2023
EHA Library, Faculty / Presenters, 400189
POVETACICEPT (ALPN-303), A POTENT DUAL BAFF/APRIL ANTAGONIST, FOR THE TREATMENT OF AUTOIMMUNE CYTOPENIAS AND OTHER ANTIBODY-RELATED DISEASES
EHA Library, Stacey Dillon, 387976
PUS1 REGULATES ERYTHROPOIESIS VIA TRNA PSEUDOURIDYLATION AND CYTOPLASMIC TRANSLATION
EHA Library, Yajing Chu, 387975
A NEW, EFFECTIVE, SAFE, NON-MYELOABLATIVE CONDITIONING REGIMEN WITH A HLA-MATCHED SIBLING DONOR FOR THE SEVERE SICKLE CELL PHENOTYPE IN ADULTS
EHA Library, Laure Joseph, 387974
LONG-TERM ERYTHROID RESPONSE DATA FROM PATIENTS (PTS) WITH NON-TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA (NTDT) RECEIVING LUSPATERCEPT IN THE BEYOND TRIAL
EHA Library, Ali Taher, 387973
SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS
EHA Library, Rongrong Liu, 387972
AN UPDATED FOLLOW-UP OF BRL-101, CRISPR-CAS9-MEDIATED GENE EDITING OF THE BCL11A ENHANCER FOR TRANSFUSION-DEPENDENT BETA-THALASSE
EHA Library, Biao Zheng, 387971
MALE PATIENTS WITH SCD HAVE A HIGHER RISK OF CEREBROVASCULAR DISEASE, INCREASED INFLAMMATORY MARKERS, AND POORER RESPONSE TO HYDROXYUREA
EHA Library, Margherita Di Mauro, 387969
INTERIM ANALYSIS OF A PHASE 2 TRIAL TO ASSESS THE EFFICACY AND SAFETY OF CRIZANLIZUMAB IN SICKLE CELL DISEASE PATIENTS WITH PRIAPISM (SPARTAN)
EHA Library, Alan Anderson, 387968
PHARMACOKINETICS/PHARMACODYNAMICS, SAFETY AND EFFICACY OF CRIZANLIZUMAB IN PATIENTS WITH SICKLE CELL DISEASE AGED 12 TO <18 YEARS: 2-YEAR DATA FROM THE PHASE 2 SOLACE-KIDS STUDY
EHA Library, Matthew Heeney, 387967
DIFFERENT MOLECULAR VASO-OCCLUSIVE TRIGGERS STIMULATE DISTINCT VASO-OCCLUSIVE PROFILES: IN VIVO RESULTS FROM MICE WITH SICKLE CELL ANEMIA
EHA Library, Lucas F. S. Gushiken, 387966
MATERNAL AND PERINATAL OUTCOMES OF SICKLE CELL DISEASE IN PREGNANCY: A NATIONWIDE STUDY IN FRANCE.
EHA Library, Laure Joseph, 387965
EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
EHA Library, Rabi Hanna, 387964
TRANSFUSION INDEPENDENCE AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA
EHA Library, Franco Locatelli, 387970

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