LONG TERM SURVIVAL IN AML PATIENTS AFTER IMMUNOTHERAPY WITH VIDIDENCEL CORRELATES WITH FUNCTIONAL T AND B-CELL RESPONSES
EHA Library, Arjan van de Loosdrecht, 419524
DENDRITIC CELL-BASED VACCINES (KSD-101) AGAINST EBV-ASSOCIATED HEMATOLOGIC NEOPLASMS: RESULTS FROM AN ONGOING PHASE I CLINICAL STUDY
EHA Library, chunrui li, 419526
IMPLICATIONS OF CAR T CELL REFERRAL AND APHERESIS DELAYS ON OUTCOMES AND TOXICITY IN LYMPHOMA PATIENTS
EHA Library, Alexander P. Boardman, 419527
SECONDARY MYELOID MALIGNANCIES FOLLOWING CAR T-CELL THERAPY FOR B-CELL MALIGNANCIES: A RETROSPECTIVE ANALYSIS
EHA Library, Amaris Balitsky, 419530
FREQUENCY OF CAR-T CELL MANUFACTURING FAILURES AND OUT-OF-SPECIFICATION PRODUCTS IN THE REAL-WORLD SETTING: A SURVEY FROM THE EBMT CELLULAR THERAPY AND IMMUNOBIOLOGY WORKING PARTY (CTIWP)
EHA Library, Nina Worel, 419532
CAR-HEMATOTOX SCORE PREDICTS OVERALL SURVIVAL IN LARGE B-CELL LYMPHOMAS TREATED WITH ANTI-CD19 CAR T-CELLS: A SUBGROUP ANALYSIS OF CART-SIE
EHA Library, Federico Stella, 419533
LONG TERM FOLLOW-UP RESULTS OF BRL-201 PHASE I STUDY, A CRISPR-BASED NON-VIRAL PD-1 LOCUS SPECIFIC INTEGRATED ANTI-CD19 CAR-T CELLS IN TREATING RELAPSED OR REFRACTORY NON-HODGKIN'S LYMPHOMA
EHA Library, Biao Zheng, 419535
TWO-YEAR FOLLOW-UP RESULTS OF C-CAR066, A NOVEL ANTI-CD20 CHIMERIC ANTIGEN RECEPTOR T-CELL THERAPY IN RELAPSED OR REFRACTORY LARGE B-CELL LYMPHOMA PATIENTS AFTER FAILURE OF CD19 CAR-T THERAPY
EHA Library, Dehui Zou, 419539
CLINICAL OUTCOMES OF PATIENTS WITH RELAPSED/REFRACTORY FOLLICULAR LYMPHOMA TREATED WITH TISAGENLECLEUCEL: PHASE 2 ELARA 3-YEAR FOLLOW-UP
EHA Library, Martin Dreyling, 419542
LONG-TERM DURABLE RESPONSES IN PATIENTS WITH R/R ALL, DLBCL, AND FL TREATED WITH TISAGENLECLEUCEL AND ITS ASSOCIATION WITH PERSISTENCE OF CHIMERIC ANTIGEN RECEPTOR (CAR) T-CELLS
EHA Library, Harald Maier, 419545
HIGH EFFICACY AND FAVORABLE SAFETY OF CD20-TARGETED CAR-T THERAPY FOR BTK INHIBITOR-REFRACTORY WALDENSTRÖM MACROGLOBULINEMIA (WM)/ LYMPHOPLASMACYTIC LYMPHOMA (LPL)
EHA Library, Brian Till, 419548
ALLOGENIC STEM CELL TRANSPLANT (SCT) AFTER CAR-T CELL THERAPY FOR RELAPSE OR REFRACTORY B-CELL PRECURSOR ACUTE LYMPHOBLASTIC LEUKEMIA (R/R B-ALL) IN PEDIATRIC PATIENTS. A SINGLE CENTER EXPERIENCE
EHA Library, Anna Alonso-Saladrigues, 419553
COMPARABLE OUTCOMES OF CD19-TARGETING CAR-T THERAPY IN TRANSFORMED FOLLICULAR LYMPHOMA AND DE NOVO DIFFUSE LARGE B-CELL LYMPHOMA
EHA Library, Alfredo Rivas-Delgado, 419555
EXPLORING PATIENT CHARACTERISTICS AND CLONAL EVOLUTION IN POST CAR-T MYELOID NEOPLASMS
EHA Library, Francesca Sillito, 419557
CD7 CAR-T THERAPY FOR PATIENTS WITH T-CELL ACUTE LYMPHOBLASTIC LEUKEMIA AND T-CELL LYMPHOBLASTIC LYMPHOMA WHO RELAPSED AFTER HEMATOPOIETIC STEM CELL TRANSPLANTATION
EHA Library, Xingyu Cao, 419559
TARGETING OPPORTUNISTIC INFECTIONS POST ALTERNATIVE-DONOR HEMATOPOIETIC CELL TRANSPLANTATION WITH PATHOGEN-SPECIFIC T CELLS
EHA Library, Anastasia Papadopoulou, 419561
C-CAR039, A NOVEL ANTI-CD20/CD19 BI-SPECIFIC CAR T-CELL THERAPY SHOWS DEEP AND DURABLE CLINICAL BENEFITS IN PATIENTS WITH RELAPSED OR REFRACTORY B-CELL NON-HODGKIN LYMPHOMA IN LONG TERM FOLLOW UP
EHA Library, Aibin Liang, 419562
CAR T-CELL THERAPY BRIDGING ALLOGENIC HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR CHILDREN WITH RELAPSED OR REFRACTORY ACUTE MYELOID LEUKEMIA
EHA Library, Zhiyong Peng, 419564
MULTICENTER ANALYSIS OF VOXELOTOR’S IMPACT ON RED BLOOD CELL TRANSFUSIONS IN PATIENTS WITH SICKLE CELL DISEASE:  RESULTS FROM A RETROSPECTIVE, REGISTRY STUDY
EHA Library, Biree Andemariam, 419565
A NOVEL ALLOSTERIC ACTIVATOR OF PYRUVATE KINASE ENHANCES HUMAN AND MOUSE ENZYMATIC ACTIVITY AND LEADS TO HEMATOLOGICAL IMPROVEMENTS IN SICKLE CELL DISEASE MOUSE MODELS
EHA Library, Mira Pochron, 419567
CHANGES IN PHYSICAL, MENTAL, AND SOCIAL HEALTH OF ADULTS WITH SICKLE CELL DISEASE FOLLOWING ALLOGENEIC STEM CELL TRANSPLANTATION: A MIXED-METHODS, PROSPECTIVE COHORT STUDY
EHA Library, Elisabeth Dovern, 419572
PHASE 1 STUDY OF SAFETY AND PHARMACOKINETICS OF CSL889 (HEMOPEXIN) IN ADULTS WITH SCD
EHA Library, Bart Biemond, 419576
ENHANCING SICKLE CELL CRISIS MANAGEMENT IN THE EMERGENCY DEPARTMENT: A MIXED-METHODS QUALITY IMPROVEMENT PROJECT
EHA Library, James Cai, 419577
IMPACT OF HYDROXYUREA ON CEREBRAL VASCULOPATHY IN CHILDREN WITH SICKLE CELL ANEMIA AFTER INITIATION FOR FREQUENT CRISES OR SEVERE ANEMIA IN ABSENCE OF ABNORMAL VELOCITIES AND ARTERIAL STENOSIS
EHA Library, Françoise Bernaudin, 419578
HEALTH-RELATED QUALITY OF LIFE IMPROVEMENTS AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH SEVERE SICKLE CELL DISEASE
EHA Library, Haydar Frangoul, 419580
THE ROLE OF INDUCIBLE NITRIC OXIDE SYNTHASE IN HYDROXYUREA IMPAIRMENT OF ANGIOGENESIS
EHA Library, Teodora Dragojević, 419581
LONG-TERM EFFECT OF VOXELOTOR ON RED BLOOD CELL TRANSFUSIONS AND VASO-OCCLUSIVE CRISES IN PATIENTS WITH SICKLE CELL DISEASE:  RESULTS FROM AN OPEN-LABEL EXTENSION OF THE PHASE 3 HOPE TRIAL
EHA Library, Richard Drachtman, 419583
HEME-INDUCED NEUTROPHIL GASDERMIN-D ACTIVATION IS SUPPRESSED BY INTERLEUKIN-27 IN SICKLE CELL DISEASE
EHA Library, Adekunle Alagbe, 419584
VACUOLES OF RED CELLS IN ASPLENIA: MERE REMAINS OR ENCHANTED APPARITIONS (OR BOTH)?
EHA Library, Lucie Dumas, 419585
HEALTH-RELATED QUALITY OF LIFE IN PEOPLE LIVING WITH SICKLE CELL DISEASE IN EUROPE: A SYSTEMATIC LITERATURE REVIEW
EHA Library, Giovanna Barcelos, 419587
CRYOPRESERVATION OF SICKLE RED BLOOD CELLS FOR COMPARISON OF OXYGENSCAN PARAMETERS BETWEEN LABORATORIES TO ENABLE DATA HARMONIZATION
EHA Library, Marissa Traets, 419588
EVALUATION OF LIVER IRON CONCENTRATION IN PATIENTS WITH SICKLE CELL DISEASE USING AUTOMATED DEEP-LEARNING ASSISTED ANALYSIS OF MAGNETIC RESONANCE IMAGES
EHA Library, Adlette Inati, 419589
FACTORS LIMITING HYDROXYCARBAMIDE DOSING IN ADULTS WITH SCD. RESULTS FROM THE UK’S SICKLE NATURAL HISTORY STUDY
EHA Library, Michael Neale, 419591
DECIPHERING THE DIFFERENT MODELS OF VASO-OCCLUSIVE EVENTS: FIRST STEPS TOWARDS A PERSONALIZED APPROACH TO THE TREATMENT OF PAINFUL VASO-OCCLUSIVE CRISIS
EHA Library, Berengere Koehl, 419592
MORTALITY AND CLINICAL COMPLICATIONS AMONG PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VOCS IN CANADA
EHA Library, Lauren Lilly, 419593
TREATMENT UTILIZATION AND CLINICAL COMPLICATIONS IN PATIENTS WITH SICKLE CELL DISEASE RECEIVING FREQUENT RED BLOOD CELL TRANSFUSIONS IN THE UNITED STATES
EHA Library, Chuka Udeze, 419594
CO-INHERITANCE OF Α-THALASSEMIA IN HBSC DISEASE CORRELATES WITH INCREASED RED BLOOD CELL DEHYDRATION AND REDUCED CLINICAL COMPLICATIONS
EHA Library, Marissa Traets, 419596
INVESTIGATING INEFFECTIVE ERYTHROPOIESIS IN A PAEDIATRIC SICKLE CELL DISEASE COHORT
EHA Library, Margherita Di Mauro, 419597
REAL-WORLD ASSESSMENT AND CLINICAL VALIDATION OF RED BLOOD CELL (RBC) HEALTH BIOMARKERS IN SICKLE CELL DISEASE (SCD)
EHA Library, Jennell White, 419598
SAFETY AND EFFICACY OF RM-001, AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS, IN TRANSFUSION-DEPENDENT Β-THALASSEMIA
EHA Library, Hui XU, 419602
INTERIM RESULTS OF GENE THERAPY USING OPTIMIZED LENTIHBBT87Q VECTOR IN FIVE CHINESE PATIENTS WITH TRANSFUSION DEPENDENT Β-THALASSEMIA
EHA Library, Nan Han, 419604
FREQUENCY, PATTERN, AND ASSOCIATIONS OF PANCREATIC IRON ACCUMULATION IN PEDIATRIC TRANSFUSION-DEPENDENT BETA-THALASSEMIA PATIENTS
EHA Library, Antonella Meloni, 419605
PHENOTYPIC CLUSTERING USING CARDIOVASCULAR MAGNETIC RESONANCE FOR RISK STRATIFICATION IN BETA-THALASSEMIA MAJOR
EHA Library, Antonella Meloni, 419606
PROGNOSTIC ROLE OF MULTIPARAMETRIC CARDIAC MAGNETIC RESONANCE IN NEO TRANSFUSION-DEPENDENT THALASSEMIA
EHA Library, Antonella Meloni, 419608
HEALTH-RELATED QUALITY OF LIFE IMPROVEMENTS AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA
EHA Library, Josu de la Fuente, 419612
IMMUNOPHENOTYPTIC ANALYSIS OF PBL FROM Β-THALASSEMIA/HEMOGLOBIN E PATIENTS FOLLOWING HYDROXYUREA THERAPY
EHA Library, Rattanawan Thubthed, 419613
TMPRSS6 INHIBITION RAPIDLY REVERSES LIVER IRON OVERLOAD AND SPLENOMEGALY IN THALASSEMIC MICE
EHA Library, Sarah Hatsell, 419614
TMPRSS6 INHIBITION IMPROVES BONE HEALTH IN B-THALASSEMIA MICE
EHA Library, Sarah Hatsell, 419619
ERYTHROPOIETIC PROTOPORPHYRIA AND X-LINKED PROTOPORPHYRIA WITH LIVER INVOLVEMENT: A CHINESE SINGLE-CENTER COHORT REPORT
EHA Library, qi wang, 419622
DESCRIPTIVE ANALYSIS OF DRUG-INDUCED IMMUNE HEMOLYTIC ANEMIA REPORTED TO THE NATIONAL PHARMACOVIGILANCE DATABASE BETWEEN 2010 AND 2022.
EHA Library, Sylvain Audia, 419626
INATICABTAGENE AUTOLEUCEL(CNCT19) IN RELAPSED OR REFRACTORY B-CELL LYMPHOMA: RESULTS OF A PHASE I CLINICAL TRIAL
EHA Library, Wei Liu, 419525
IMMUNE RECONSTITUTION FOLLOWING CD19 CAR-T FOR R/R B-NHL IS ASSOCIATED WITH IMPROVED SURVIVAL OUTCOMES AND IS IMPAIRED AT TIME OF POST-CAR-T PROGRESSION
EHA Library, Sophia Stock, 419528
IMMUNOGENETIC PROFILING OF EX VIVO GENERATED PATHOGEN-SPECIFIC T CELLS FOR IMMUNOTHERAPY OF OPPORTUNISTIC INFECTIONS POST ALLOGENEIC HEMATOPOIETIC CELL TRANSPLANTATION
EHA Library, Chrysa Pantazi, 419529
POINT-OF-CARE NON-VIRAL PRODUCTION OF CD19 CHIMERIC ANTIGEN RECEPTOR-T CELLS WITH ENHANCED TSCM IMMUNOPHENOTYPE FOR THERAPY OF REFRACTORY B-CELL MALIGNANCIES- PRELIMINARY RESULTS OF PHASE I CLINICAL TRIAL
EHA Library, Pavel Otáhal, 419534
CAR T TREATMENT ACCESS AND OUTCOMES IN PATIENTS WITH LARGE B-CELL LYMPHOMA ACCORDING TO ETHNICITY AND SOCIOECONOMIC DEPRIVATION IN THE UK
EHA Library, Oana Diana Dragoi, 419536
CHANGING THE NATURAL HISTORY OF PYRUVATE KINASE DEFICIENCY WITH LENTIVIRAL-MEDIATED GENE THERAPY: RESULTS OF A GLOBAL PHASE 1 STUDY
EHA Library, Julian Sevilla, 419537
EARLY AND LATE INTRODUCTION OF CAR T-CELL THERAPY IN LARGE B-CELL LYMPHOMA HAVE COMPARABLE TOXICITY AND EFFICACY OUTCOMES
EHA Library, Magdalena Corona de Lapuerta, 419538
FIRST RESULTS OF A COMPREHENSIVE PROSPECTIVE PROTOCOL OF RADIOTHERAPY BRIDGING AND CONSOLIDATION FOR CAR T IN LARGE B-CELL LYMPHOMA (RESTART)
EHA Library, Christianne Bourlon, 419541
ASSOCIATION BETWEEN BODY MASS INDEX AND OUTCOMES OF CAR-T THERAPY ACROSS HEMATOLOGIC MALIGNANCIES
EHA Library, Yannis Valtis, 419543
AFTER PROPENSITY SCORE WEIGHTING AXICABTAGENE CILOLEUCEL CONFER SUPERIOR PROGRESSION-FREE SURVIVAL COMPARED TO TISAGENLECLEUCEL IN LARGE B-CELL LYMPHOMAS: FINAL RESULTS OF THE ITALIAN CART-SIE STUDY
EHA Library, Federico Stella, 419544
FIRST REAL-WORLD EXPERIENCE OF COMMERCIAL RELMACABTAGENE AUTOLEUCEL (RELMA-CEL) FOR RELAPSED/REFRACTORY CENTRAL NERVOUS SYSTEM LYMPHOMA: A MULTICENTER RETROSPECTIVE ANALYSIS OF PATIENTS IN CHINA
EHA Library, Wenyan Yu, 419546
INB-100: PILOT STUDY OF DONOR DERIVED, EX-VIVO EXPANDED/ACTIVATED GAMMA-DELTA T CELL INFUSION FOLLOWING HAPLOIDENTICAL HEMATOPOIETIC STEM-CELL TRANSPLANTATION  AND POST-TRANSPLANT CYCLOPHOSPHAMIDE
EHA Library, Joseph McGuirk, 419547
HEMATOPOIETIC STEM CELL GENE THERAPY FOR HURLER SYNDROME: INTERIM SKELETAL, NEUROLOGICAL AND SYSTEMIC OUTCOMES
EHA Library, Maria Ester Bernardo, 419549
CHIMERIC ANTIGEN RECEPTOR T-CELL THERAPY IS FEASIBLE IN PATIENTS 80 YEARS OF AGE OR OLDER WITH B-CELL LYMPHOMA: A US MULTICENTER COLLABORATIVE STUDY
EHA Library, Julio Chavez, 419550
SINGLE CELL ANALYSIS REVEALS THAT T CELLS AND MONOCYTES CONTRIBUTE TO RESPONSE AND EARLY PROGRESSION RESPECTIVELY IN FOLLICULAR LYMPHOMA PATIENTS TREATED WITH PEMBROLIZUMAB
EHA Library, Zhi-Zhang Yang, 419554
DROPLET DIGITAL PCR AND FLOW CYTOMETRY SENSITIVITY FOR MEASURING CAR-T CELL KINETICS IN ADULT PATIENTS WITH RELAPSED/REFRACTORY B CELL ACUTE LYMPHOBLASTIC LEUKEMIA TREATED WITH OBECABTAGENE AUTOLEUCEL
EHA Library, Claire Roddie, 419556
PHASE I STUDY OF AN ANTI-CD7 UNIVERSAL CAR-T THERAPY FOR PATIENTS WITH RELAPSED/REFRACTORY CD7 POSITIVE T-ALL/LBL
EHA Library, He Huang, 419558
CD7.PEBL-CART FOR PATIENTS WITH RELAPSED/REFRACTORY T-CELL ACUTE LYMPHOBLASTIC LEUKEMIA
EHA Library, Marco Becilli, 419560
RENI-CEL, THE FIRST ASCAS12A GENE-EDITED CELL THERAPY, SHOWS PROMISING PRELIMINARY RESULTS IN KEY CLINICAL OUTCOMES IN TRANSFUSION-DEPENDENT BETA-THALASSEMIA PATIENTS TREATED IN THE EDITHAL TRIAL
EHA Library, Haydar Frangoul, 419563
ROBUST AUTOLOGOUS CD34+ HSPC MANUFACTURING WITH A CLOSED AND AUTOMATED PROCESS OPTIMIZED FOR PATIENTS WITH SICKLE CELL DISEASE
EHA Library, Paul Kopesky, 419566
GMI-1687-101, A PHASE 1A FIRST IN HUMAN TRIAL OF SECOND-GENERATION E-SELECTIN ANTAGONIST GMI-1687
EHA Library, Jay Lozier, 419568
FACTORS DRIVING PARTICIPATION IN CLINICAL TRIALS AMONG PEOPLE WITH SICKLE CELL DISEASE DIFFER IN IMPORTANCE ACROSS GEOGRAPHIC REGIONS: FINDINGS FROM THE GLOBAL LISTEN SURVEY
EHA Library, Raffaella Colombatti, 419569
ADHERENCE, TREATMENT USE, AND CLINICAL OUTCOMES IN PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VASO-OCCLUSIVE CRISES TREATED WITH L-GLUTAMINE, VOXELOTOR, OR CRIZANLIZUMAB IN THE UNITED STATES
EHA Library, Chuka Udeze, 419570
THE EFFECT OF RED BLOOD CELL EXCHANGE ON ECHOCARDIOGRAPHIC FINDINGS IN SCD
EHA Library, Jules M.Ross, 419571
HYDROXYUREA MODULATES VLA-4 BINDING TO VCAM-1 THROUGH ERYTHROID SIGNALING PATHWAYS INDEPENDENT OF ADHESION RECEPTOR EXPRESSION IN PRIMARY CULTURES OF SICKLE ERYTHROBLASTS
EHA Library, Moira Lancelot, 419573
REAL-WORLD IMPLEMENTATION OF THE DAVID-CAROLL BUPRENORPHINE PROTOCOL FOR PAIN MANAGEMENT IN SICKLE CELL DISEASE
EHA Library, Najibah Galadanci, 419574
SURVIVAL RATES OF A COHORT OF ADULTS WITH SICKLE CELL DISEASE BY BASELINE HEMOGLOBIN VALUES OVER A 10-YEAR FOLLOW-UP PERIOD
EHA Library, Pablo Bartolucci, 419579
PHYSICIANS’ PERCEPTIONS OF BARRIERS TO PRESCRIBING SICKLE CELL DISEASE TREATMENTS IN THE UNITED STATES
EHA Library, Aine Kyle, 419582
EFFECT OF VOXELOTOR ON CEREBRAL PERFUSION AND CEREBRAL OXYGENATION IN ADULT PATIENTS WITH SICKLE CELL DISEASE; 12 MONTH FOLLOW UP
EHA Library, Kadère Konté, 419586
RISK FACTORS FOR MULTIPLE ORGAN DAMAGES IN A COHORT OF INDIAN SICKLE CELL DISEASE PATIENTS
EHA Library, Nikhil Shinde, 419590
ALL-CAUSE ANAEMIA TRUMPS DEGREE OF HAEMOLYSIS AS A DETERMINANT OF QUALITY OF LIFE: THE UK MULTI-SITE SICKLE NATURAL HISTORY STUDY
EHA Library, Jumoke Stella Okikiolu, 419595
MAPPING THE PRODROMAL STAGE OF VASO-OCCLUSIVE CRISES: A PATIENT EXPERIENCE AND WEARABLE BIOMETRICS-DRIVEN APPROACH
EHA Library, Kim Summers, 419599
THE EARLY MYELOID COMMITMENT OF HSPCS IN SICKLE CELL ANEMIA IS ASSOCIATED WITH ABERRANT DIFFERENTIATION TO THE MONOCYTIC LINEAGE
EHA Library, Berengere Koehl, 419600
EFFICACY AND SAFETY OF BRL-101, CRISPR-CAS9-MEDIATED GENE EDITING OF THE BCL11A ENHANCER IN TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA
EHA Library, Biao Zheng, 419601
SAFETY DATA FROM THE DOSE-FINDING COHORTS: A PHASE 2A STUDY OF LUSPATERCEPT IN PEDIATRIC PATIENTS WITH ΒETA-THALASSEMIA
EHA Library, Antonis Kattamis, 419603
EXPLORING THE REAL-LIFE EFFICACY AND SAFETY OF LUSPATERCEPT WITH A MIXED PATTERN STUDY
EHA Library, Yesim Aydinok, 419607
CHARACTERIZING PATTERNS OF TRANSFUSION BURDEN (TB) REDUCTION IN PATIENTS (PTS) WITH TRANSFUSION-DEPENDENT (TD) ΒETA-THALASSEMIA TREATED WITH LUSPATERCEPT IN THE BELIEVE TRIAL
EHA Library, Kevin Kuo, 419609
ANALYSIS OF ERYTHROPOIESIS AND IRON METABOLISM IN A COHORT OF Β-THALASSEMIA PATIENTS TREATED WITH LUSPATERCEPT
EHA Library, Nicolò Tesio, 419610
UNRELATED DONOR TRANSPLANTATION OFFERS A REAL CURATIVE OPPORTUNITY FOR PATIENTS WITH TRANSFUSION-DEPENDENT THALASSEMIA. EXPERIENCE OF THE SPANISH GROUP FOR BONE MARROW TRANSPLANTATION IN CHILDREN
EHA Library, Maribel Benítez Carabante, 419611
AVAILABILITY AND USE OF IMAGING TECHNIQUES FOR MANAGEMENT OF HAEMOGLOBINOPATHIES IN ITALIAN NETWORK: PRELIMINARY RESULTS OF A SURVEY BY ITALIAN SOCIETY OF THALASSAEMIA AND HAEMOGLOBINOPATHIES (SITE)
EHA Library, Gian Luca Forni, 419615
IMPROVEMENTS IN FATIGUE AND 6-MINUTE WALK TEST IN ADULTS WITH ALPHA- OR BETA-NON–TRANSFUSION-DEPENDENT THALASSEMIA: THE PHASE 3 ENERGIZE TRIAL OF MITAPIVAT
EHA Library, Kevin H. M. Kuo, 419616
PREDICTING AND EVALUATING RESPONSE TO LUSPATERCEPT IN TRANSFUSION-DEPENDENT Β-THALASSEMIA: NEW INSIGHT FROM A REAL-LIFE EXPERIENCE.
EHA Library, Daniele Lello Panzieri, 419617
IN VITRO MODELLING OF Β0-THALASSAEMIA: A CELLULAR PLATFORM ENABLING EXPERIMENTAL AND THERAPEUTIC INVESTIGATIONS
EHA Library, Jim Vadolas, 419618
GENOTYPE AND PHENOTYPE CORRELATION IN Β-THALASSEMIA IN GREECE: THE EXPERIENCE OF AN ADULT CENTER.
EHA Library, Maria Dimopoulou, 419620
ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION VERSUS BLOOD TRANSFUSION AND IRON CHELATION ON PATIENT QUALITY OF LIFE IN TRANSFUSION-DEPENDENT THALASSEMIA: A META-ANALYSIS OF OBSERVATIONAL STUDIES
EHA Library, Tsampika Vasileia Kalamara, 419621
REAL-WORLD EXPERIENCE OF IMMUNOCHEMOTHERAPY IN COLD AGGLUTININ DISEASE AND COLD AGGLUTININ SYNDROME
EHA Library, Femke Mulder, 419623
HEREDITARY STOMATOCYTOSIS (HST):EXPERIENCE IN A PEDIATRIC TERTIARY CARE CENTER IN ARGENTINA
EHA Library, Estefania Rossetti, 419624
ADDING THROMBOPOIETIN RECEPTOR AGONIST TO INTENSIVE IMMUNOSUPPRESSIVE THERAPY HELPS ADULT PATIENTS CATCH UP PEDIATRIC PATIENTS IN SEVERE APLASTIC ANEMIA 翻译 搜索 复制
EHA Library, Bixi Yang, 419625
INVESTIGATING NON-IMMUNE HEMOLYTIC ANEMIA IN CLONAL HEMATOPOIESIS OF INDETERMINATE POTENTIAL (CHIP) AND CLONAL CYTOPENIAS OF UNDETERMINED SIGNIFICANCE (CCUS)
EHA Library, Hadiyah Ahmad, 419627
RETICULOCYTES OF SPLENECTOMIZED PATIENTS WITH HEREDITARY SPHEROCYTOSIS - MRNA LEVELS OF ANTIOXIDANT ENZYMES
EHA Library, Daniela Melo, 419628

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