MANAGEMENT OF IMMUNE EFFECTOR CELL-ASSOCIATED NEUROTOXICITY SYNDROME FOLLOWING CAR-T CELL THERAPY IN CLINICAL PRACTICE: A MULTICENTRIC, RETROSPECTIVE, REAL-WORLD ANALYSIS OF TREATMENT APPROACHES AND OUTCOMES
EHA Library, Veit Bücklein,
4161223
POCIREDIR, A POTENT AND SELECTIVE EED INHIBITOR FOR THE TREATMENT OF SICKLE CELL DISEASE, INDUCES TARGET ENGAGEMENT AND GENE EXPRESSION CHANGES THAT ARE SPECIFIC AND REVERSIBLE IN WILD-TYPE MICE
EHA Library, Caterina Minniti,
4161249
PATIENT-REPORTED VASO-OCCLUSIVE EVENTS, THEIR ASSOCIATED PAIN SEVERITY, AND IMPACT OF SICKLE CELL DISEASE ON FATIGUE AND QUALITY OF LIFE: A REAL-WORLD SURVEY IN THE UNITED STATES
EHA Library, Oladipo Cole,
4161253
UPDATED SAFETY AND EFFICACY RESULTS OF RM-001, AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS, IN TREATING TRANSFUSION-DEPENDENT ß-THALASSEMIA
EHA Library, Hui Xu,
4161255