A PHASE 1, RANDOMIZED, PARTICIPANT- AND INVESTIGATOR-BLINDED, PLACEBO-CONTROLLED STUDY TO EXPLORE THE SAFETY AND PHARMACOKINETICS OF SUPRATHERAPEUTIC MULTIPLE DOSES OF IPTACOPAN IN HEALTHY VOLUNTEERS
EHA Library, Robert Schmouder,
4162701
EFGARTIGIMOD IV FOR THE TREATMENT OF PRIMARY IMMUNE THROMBOCYTOPENIA: A PLANNED, PHASE 3, RANDOMIZED, DOUBLE-BLINDED, PLACEBO-CONTROLLED, PARALLEL-ARM STUDY WITH OPEN-LABEL PERIOD (ADVANCE NEXT)
EHA Library, Monica Carpenedo,
4162741
POST-DISCHARGE INSIGHTS IN SICKLE CELL DISEASE: EVALUATING COMPLICATIONS, SYMPTOMS, AND QUALITY OF LIFE THROUGH DIGITALLY CAPTURED PATIENT EXPERIENCES, PATIENT-REPORTED OUTCOMES, AND WEARABLE BIOMETRICS.
EHA Library, Kim Summers,
4162899