DXO-1801, A HEPATOCYTE-TARGETED GALNAC-SIRNA, DEMONSTRATES HEPCIDIN PATHWAY MODULATION, IRON MOBILIZATION, AND A FAVORABLE SAFETY PROFILE IN NON-HUMAN PRIMATES
EHA Library, Lilach Steiner,
4208952
A SINGLE CENTER AUDIT ON THE USE OF BLOOD PRODUCTS INCLUDING RED CELLS, PLATELETS, FRESH FROZEN PLASMA AND CRYOPRECIPITATE IN A TERTIARY NEONATAL UNIT- THE UNIVERSITY COLLEGE LONDON HOSPITAL
EHA Library, Devi Purushothaman,
4208982
A REAL-WORLD STUDY ON THE EFFICACY, SAFETY, AND UTILIZATION OF A CHINESE-DEVELOPED RECOMBINANT FACTOR VIII ( SCT800) FOR PROPHYLACTIC TREATMENT IN MODERATE TO SEVERE HAEMOPHILIA A PATIENTS
EHA Library, Feng Xue,
4209010
DOUBLE-BLIND, RANDOMIZED, PLACEBO-CONTROLLED STUDY OF CROVALIMAB FOR THE TREATMENT OF ACUTE VASO-OCCLUSIVE EPISODES IN SICKLE CELL DISEASE: RESULTS OF THE PHASE 1B CROSSWALK-A TRIAL
EHA Library, Satheesh Chonat,
4208919
ADJUNCT RESVERATROL OR OMEPRAZOLE IN NON-TRANSFUSION DEPENDENT THALASSEMIA PATIENTS WITH SECONDARY HEMOCHROMATOSIS: A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED TRIAL
EHA Library, Thanapong Chopetgool,
4208939
INTACT COVID-19 VACCINATION RESPONSE AND OVERALL SAFETY IN THE PHASE 3, MULTICENTER, DOUBLE-BLINDED, PLACEBO-CONTROLLED, RANDOMIZED CLINICAL TRIAL OF INTRAVENOUS EFGARTIGIMOD IN ITP (ADVANCE IV)
EHA Library, Monica Carpenedo,
4208989
EFFECTS OF IANALUMAB TREATMENT ON B CELL ACTIVATION, MATURATION, AND MAINTENANCE OF VACCINE TITERS IN PATIENTS WITH PRIMARY IMMUNE THROMBOCYTOPENIA IN THE PHASE 2 VAYHIT3 STUDY
EHA Library, Thomas Stauch,
4209000
EVOLVING TREATMENT PRIORITIES IN HEMOPHILIA: PHYSICIAN AND PATIENT PERSPECTIVES ON CONVENIENCE, QUALITY OF LIFE, AND THE EMERGING ROLE OF REBALANCING AGENTS ACROSS THE US AND EU5
EHA Library, Sarah Hendry,
4209012