CHARACTERIZATION OF STAT5B MUTATIONS AND TCRΒ REPERTOIRE IN CD4+ T LARGE GRANULAR LYMPHOCYTE LEUKEMIA
EHA Library, Antonella Teramo, 325371
AUTOPHAGY-RELATED GENETIC VARIANTS INFLUENCE THE RISK OF DEVELOPING CHRONIC LYMPHOCYTIC LEUKEMIA: A STUDY IN THE CONTEXT OF THE CRUCIAL CONSORTIUM
EHA Library, Ana Moñiz Díez, 325372
ANALYSIS OF GENOMIC COMPLEXITY IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) USING OPTICAL GENOME MAPPING
EHA Library, Anna Puiggros, 325376
THE IDO-KYN-AHR PATHWAY PROMOTES CHRONIC LYMPHOCYTIC LEUKEMIA CELLS SURVIVAL AND MITIGATES THE APOPTOTIC EFFECT OF ABT-199
EHA Library, Claudio Giacinto Atene, 325377
LNCRNA LANDSCAPE ANALYSIS IDENTIFIED LNCRNA LEF-AS1 AS AN ONCOGENE THAT UPREGULATES LEF1 AND PROMOTES SURVIVAL IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Lei Fan, 325378
SOMATIC HYPERMUTATION PROFILES IN STEREOTYPED IGHV4-34 RECEPTORS FROM SOUTH AMERICAN CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Carmen Stanganelli, 325385
NGS APPROACH FOR IGHV REARRANGEMENT ANALYSIS IN CLL PATIENTS WITH OLIGOCLONAL DISEASE
EHA Library, Bella Biderman, 325386
OTHER MALIGNANCIES IN THE HISTORY OF CHRONIC LYMPHOCYTIC LEUKEMIA – A RETROSPECTIVE, MULTICENTER COHORT STUDY BY ERIC, THE EUROPEAN RESEARCH INITIATIVE ON CLL, IN HARMONY
EHA Library, Thomas Chatzikonstantinou, 325391
VENETOCLAX-OBINUTUZUMAB MODULATES CLONAL GROWTH: RESULTS OF A POPULATION-BASED MINIMAL RESIDUAL DISEASE MODEL FROM THE RANDOMIZED CLL14 STUDY
EHA Library, Othman Al-Sawaf, 325392
PIRTOBRUTINIB (LOXO-305), A NEXT GENERATION, HIGHLY SELECTIVE, NON-COVALENT BTK INHIBITOR IN PREVIOUSLY TREATED CLL/SLL: RESULTS FROM THE PHASE 1/2 BRUIN STUDY
EHA Library, Lindsey Roeker, 325393
MINIMAL RESIDUAL DISEASE-DRIVEN TREATMENT INTENSIFICATION WITH SEQUENTIAL ADDITION OF IBRUTINIB (IBR) TO VENETOCLAX (VEN) IN RELAPSED/REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA (CLL): THE IMPROVE STUDY
EHA Library, Lydia Scarfò, 325394
IBRUTINIB TREATMENT IN THE FIRST-LINE SETTING FOR PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: UP TO 7 YEARS OF FOLLOW-UP IN THE RESONATE-2 STUDY
EHA Library, Paolo Ghia, 325396
TG-1701, A SELECTIVE BRUTON TYROSINE KINASE (BTK) INHIBITOR, AS MONOTHERAPY AND IN COMBINATION WITH UBLITUXIMAB AND UMBRALISIB (U2) IN CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) AND LYMPHOMA
EHA Library, Chan Y. Cheah, 325398
SYSTOLIC FUNCTION OF THE LEFT VENTRICULAR MYOCARDIAL IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA RECEIVING IBRUTINIB.
EHA Library, Elena Emelina, 325401
PRELIMINARY RESULTS OF THE PHASE 2 STUDY OF ZANUBRUTINIB IN PATIENTS WITH PREVIOUSLY TREATED B-CELL MALIGNANCIES INTOLERANT TO IBRUTINIB AND/OR ACALABRUTINIB
EHA Library, Mazyar Shadman, 325402
A PHASE 1A/B DOSE ESCALATION STUDY OF THE MUTATION AGNOSTIC BTK/FLT3 INHIBITOR LUXEPTINIB (CG-806) IN PATIENTS WITH RELAPSED OR REFRACTORY B-CELL MALIGNANCIES
EHA Library, Rafael Bejar, 325403
REAL-WORLD EFFICACY AND SAFETY OF VENETOCLAX IN CHRONIC LYMPHOCYTIC LEUKAEMIA – FIRST DATA FROM THE VERONE STUDY, IN PATIENTS WITH VENETOCLAX MONOTHERAPY
EHA Library, Loic Ysebaert, 325406
MOLTO, A MULTICENTER, OPEN LABEL, UNCONTROLLED, PHASE II CLINICAL TRIAL ON SAFETY AND EFFICACY OF VENETOCLAX, ATEZOLIZUMAB AND OBINUTUZUMAB IN RICHTER TRANSFORMATION OF CLL: SAFETY INTERIM ANALYSIS
EHA Library, Anna Maria Frustaci, 325410
LEUKEMIA CUTIS IN CHRONIC LYMPHOCYTIC LEUKEMIA: A RETROSPECTIVE STUDY OF THE FRENCH INNOVATIVE LEUKEMIA ORGANIZATION (FILO)
EHA Library, Gregory Lazarian, 325412
EFFECTIVENESS AND SAFETY OF IBRUTINIB IN CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) AND MANTLE CELL LYMPHOMA (MCL) IN BELGIAN ROUTINE CLINICAL PRACTICE WITH A 3-YEAR FOLLOW-UP
EHA Library, Ann Janssens, 325414
PROFILES OF NK CELL SUBSETS ARE ASSOCIATED WITH SUCCESSFUL TYROSINE KINASE INHIBITOR DISCONTINUATION IN CHRONIC MYELOID LEUKEMIA AND CHANGE FOLLOWING INTERFERON TREATMENT
EHA Library, Hao Jiang, 325416
AGE-RELATED DNA DAMAGE RESPONSE (DDR) IN HEMATOPOIETIC STEM CELLS FROM CHRONIC MYELOID LEUKAEMIA PATIENTS WHO ATTEMPTED TKI DISCONTINUATION.
EHA Library, Chiara Manfroni, 325418
ASSESSMENT OF LEUKEMIC STEM CELL CD26+ IN CHRONIC MYELOID LEUKEMIA PATIENTS WITH DEEP MOLECULAR RESPONSE.
EHA Library, Raquel Bengió, 325419
EUTOS EXPERIENCE OF STANDARDISATION OF MOLECULAR MONITORING FOR CML (2016 – 2020). USE OF SECONDARY BCR-ABL1 REFERENCE MATERIALS FOR CONVERSION FACTOR VALIDATION AND ASSESSMENT OF MR4.5 DETECTION
EHA Library, Helen White, 325420
COMPREHENSIVE IMMUNOPROFILE OF NK CELLS FROM CML PATIENTS IN TFR REVEALS A POSSIBLE ROLE OF MEMORY-LIKE NK CELLS
EHA Library, Maria Belen Sanchez, 325423
TARGETING THE LEUKEMIC STEM CELL NICHE BY PI3K INHIBITORS IN CHRONIC MYELOID LEUKEMIA TO OVERCOME LEUKEMIC STEM CELL RESISTANCE
EHA Library, Yüksel Filik Schüppler, 325424
RARE MUTATIONS IN BCR-ABL THE KINASE DOMAIN IN CRONIC MYELOID LEUKEMIA PATIENTS.
EHA Library, Rocío Delamer, 325425
SECOND-LINE BOSUTINIB FOR PATIENTS WITH CHRONIC PHASE CHRONIC MYELOID LEUKEMIA : FINAL 10-YEAR RESULTS OF A PHASE 1/2 STUDY
EHA Library, Carlo Gambacorti-Passerini, 325432
TREATMENT-FREE REMISSION IN CHRONIC MYELOID LEUKEMIA PATIENTS TREATED WITH LOW-DOSE TKIS. A FEASIBLE OPTION ALSO IN THE REAL-LIFE SETTING?
EHA Library, Alessandra Iurlo, 325433
COVID-19 IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA: DISEASE OUTCOMES AND FIRST VACCINATION DATA IN RUSSIAN FEDERATION
EHA Library, Ekaterina Chelysheva, 325434
ASSOCIATION OF CREATINE KINASE ELEVATION WITH CLINICAL OUTCOMES IN CHRONIC MYELOID LEUKEMIA
EHA Library, Aniket Bankar, 325435
EFFECT OF COMORBIDITIES ON PATIENT RESPONSES WITH FIRST-LINE DASATINIB VERSUS IMATINIB IN CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE: EXPLORATORY POST HOC ANALYSIS OF DASISION
EHA Library, Breccia Massimo, 325437
HYDROXYUREA PRE-TREATMENT IN CHRONIC MYELOID LEUKEMIA PATIENTS: MORE HARM THAN GOOD?
EHA Library, Camille C.B. Kockerols, 325438
TREATMENT ADHERENCE IN CHRONIC MYELOID LEUKEMIA PATIENTS RECEIVING TYROSINE KINASE INHIBITORS
EHA Library, S.M.Amine BENLAZAR, 325443
THE EFFECT OF BODY MASS INDEX ON EFFICACY AND SAFETY OF BOSUTINIB OR IMATINIB IN PATIENTS WITH NEWLY DIAGNOSED CHRONIC MYELOID LEUKEMIA
EHA Library, Tim Brümmendorf, 325444
EFFICACY AND SAFETY RESULTS FROM AN OPEN-LABEL PHASE 2 STUDY OF PARSACLISIB FOR THE TREATMENT OF AUTOIMMUNE HEMOLYTIC ANEMIA (AIHA)
EHA Library, Wilma Barcellini, 325445
RARE ANEMIA DISORDERS EUROPEAN EPIDEMIOLOGICAL PLATFORM (RADEEP): DISTRIBUTION OF PATIENTS AFFECTED BY PYRUVATE KINASE DEFICIENCY IN EUROPE
EHA Library, Maria Del Mar Mañú Pereira, 325446
FOSTAMATINIB FOR THE TREATMENT OF WARM ANTIBODY AUTOIMMUNE HEMOLYTIC ANEMIA (WAIHA): UPDATES FROM THE PHASE 2 AND PHASE 3 CLINICAL TRIALS
EHA Library, Dheepika Weerasinghe, 325447
INHIBITION OF COMPLEMENT C1S WITH SUTIMLIMAB IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): 1-YEAR INTERIM RESULTS OF THE PHASE 3 CARDINAL STUDY LONG-TERM FOLLOW-UP
EHA Library, Alexander Röth, 325449
CANCER RISK IN PATIENTS WITH WARM AUTOIMMUNE HAEMOLYTIC ANAEMIA - A NATIONWIDE COHORT STUDY
EHA Library, Stinne Tranekaer, 325450
PHARMACOLOGIC INHIBITION OF PI3KΔ REDUCES AUTOANTIBODY FORMATION AND IS EFFICACIOUS IN A PRECLINICAL MODEL OF AUTOIMMUNE HEMOLYTIC ANEMIA
EHA Library, Paul Smith, 325453
MITAPIVAT AMELIORATES RED CELL FEATURES AND DECREASES ANEMIA IN BAND 4.2-/- MICE, A MODEL OF HEREDITARY SPHEROCYTOSIS
EHA Library, Alessandro Matte, 325455
WARM AUTOIMMUNE HEMOLYTIC ANEMIA IS ASSOCIATED WITH A REGULATORY T CELL DEFICIENCY AND A TH17 POLARIZATION
EHA Library, Marion Ciudad, 325457
MOLECULAR HETEROGENEITY OF GLUCOSE-6-PHOSPHATE DEHYDROGENASE (G6PD) DEFICIENCY IN PORTUGAL
EHA Library, Licinio Manco, 325460
SYMPTOMATIC BONE MARROW RECONVERSION: A COMMON FEATURE IN HEREDITARY SPHEROCYTOSIS ?
EHA Library, Camille Pochard, 325461
SOLUBLE CTLA-4 IN CHILDREN WITH IMMUNE CYTOPENIAS: RELATION TO DISEASE ACTIVITY
EHA Library, Sara Makkeyah, 325462
IDENTIFICATION OF A WARM AUTOIMMUNE HEMOLYTIC ANEMIA (WAIHA) POPULATION USING PREDICTIVE ANALYTICS OF A KNOWN CLINICALLY PROFILED COHORT
EHA Library, Keith McCrae, 325463
AUTOIMMUNE HEMOLYTIC ANEMIA ASSOCIATED WITH LYMPHOID MALIGNANCIES: REPORT FROM A FRENCH PROSPECTIVE REGISTER.
EHA Library, Sylvain Audia, 325465
CLINICAL AND MOLECULAR CHARACTERISTICS OF IMERSLUND‐GRÄSBECK SYNDROME: FIRST REPORT OF A NOVEL FRAMESHIFT VARIANT IN EXON 11 OF AMN GENE
EHA Library, Mohamed Elshinawy, 325467
INFLAMMATION AND FATIGUE IN PATIENTS WITH COLD AGGLUTININ DISEASE (CAD): ANALYSIS FROM THE PHASE 3 CARDINAL STUDY
EHA Library, Ilene Weitz, 325469
THE GUT MICROBIOME IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Tereza Faitova, 325373
EX VIVO DRUG SENSITIVITY IDENTIFIES COMBINATION TREATMENT WITH PI3K/BCL-2 INHIBITORS FOR MONOTHERAPY-REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Sigrid Skanland, 325374
THE IGLV3-21 LIGHT CHAIN ANALYSIS IN CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Nadiia Bilous, 325375
DISCOVERY OF HBW-3-10: A POTENT, ORALLY ACTIVE, REVERSIBLE BRUTON’S TYROSINE KINASE (BTK) INHIBITOR WITH ANTITUMOR ACTIVITIES IN MICE
EHA Library, Chester Yuan, 325379
TARGETING CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) CELLS WITH THE GLYCOGEN SYNTHASE KINASE-3 BETA (GSK-3Β)-SELECTIVE SMALL MOLECULE INHIBITOR, 9-ING-41
EHA Library, Estevao Carlos Silva Barcelos, 325380
INFLUENCE OF POLYMORPHISMS OF CODON 72 OF TP53 IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Martin-Antonio Cabero-Becerra, 325381
CRISPR/CAS9 AND MRNA-BASED GENE EDITING AND EXPRESSION IN CHRONIC LYMPHOCYTIC LEUKEMIA CELLS
EHA Library, Anna Kabanova, 325382
THE SIGNS OF NEGATIVE SELECTION IN IGHV FRAMEWORK REGIONS ARE ASSOCIATED WITH WORSE OVERALL SURVIVAL OF CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS
EHA Library, Iryna Abramenko, 325383
GENE EXPRESSION MODEL TO IDENTIFY CHRONIC LYMPHOCYTIC LEUKEMIA (CLL) PATIENTS WITH AN ULTRA-STABLE DISEASE. A CAMPUS CLL STUDY.
EHA Library, Ilaria Del Giudice, 325384
SYSTEMATIC TRANSCRIPTOME ANALYSIS REVEALS DISTINCT COMPETING ENDOGENOUS RNA NETWORK IN CHRONIC LYMPHOCYTIC LEUKEMIA
EHA Library, Ya Zhang, 325387
CHRONIC LYMPHOCYTIC LEUKAEMIA (CLL): HIGH-RISK DATA FROM AN IRISH POPULATION.
EHA Library, Carmel Waldron, 325388
INFLUENCE OF INFLAMMATORY CYTOKINES ON S100A PROTEINS EXPRESSION IN CLL PATIENTS
EHA Library, Olivera Mitrovic, 325389
RELEVANCE OF NRF2/KEAP1 AXIS IN CHRONIC LYMPHOCYTIC LEUKEMIA DEVELOPMENT
EHA Library, Ana Ribeiro, 325390
REAL-WORLD APPLICATION OF NATIONAL COMPREHENSIVE CANCER NETWORK CLINICAL PRACTICE GUIDELINES IN ONCOLOGY (NCCN GUIDELINES®) FOR CLL/SLL FROM THE INFORMCLL REGISTRY
EHA Library, Jacqueline Barrientos, 325395
SECOND PRIMARY MALIGNANCIES IN PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: A NATIONWIDE, POPULATION-BASED STUDY IN THE NETHERLANDS
EHA Library, Lina Van Der Straten, 325397
ZANUBRUTINIB MONOTHERAPY IN PATIENTS WITH RELAPSED OR REFRACTORY CHRONIC LYMPHOCYTIC LEUKEMIA: 34-MONTH FOLLOW-UP RESULTS
EHA Library, Wei Xu, 325399
CONDITIONAL RELATIVE SURVIVAL AMONG PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA: A NATIONWIDE, POPULATION-BASED STUDY IN THE NETHERLANDS
EHA Library, Lina Van Der Straten, 325400
TEN-YEAR FOLLOW-UP OF 415 CLL PATIENTS TREATED WITH FLUDARABINE CYCLOPHOSPHAMIDE-BASED CHEMOIMMUNOTHERAPY IN THE FRONTLINE ARCTIC AND ADMIRE TRIALS, A COMPREHENSIVE ASSESSMENT OF PROGNOSTIC FACTORS
EHA Library, David Allsup, 325404
OUTCOME OF 100 TP53-DISRUPTED CHRONIC LYMPHOCYTIC LEUKEMIA PATIENTS TREATED FRONT-LINE WITH IBRUTINIB. A REAL-LIFE CAMPUS CLL STUDY.
EHA Library, Andrea Visentin, 325405
POTENTIAL CAPABILITIES OF MRNA ROR1 AND MIR-155 FOR MRD ASSESSMENT IN CLL
EHA Library, Marina Stolyar, 325407
SAFETY AND EFFECTIVENESS OF VENETOCLAX IN COMBINATION WITH RITUXIMAB IN ELDERLY PATIENTS WITH RELAPSED/REFRACTORY CLL TREATED UNDER REAL-LIFE CONDITIONS – DATA FROM THE OBSERVATIONAL STUDY VERVE
EHA Library, Ingo Schwaner, 325408
COMPARISON OF VENETOCLAX INPATIENT AND OUTPATIENT RAMP-UP STRATEGIES FOR CLL. UK MULTICENTRE RESTROSPECTIVE STUDY
EHA Library, Rocío Figueroa Mora, 325409
TREATMENT OF CLL RELAPSED/REFRACTORY PATIENTS IN COVID-19 PANDEMIC: A REAL-LIFE EXPERIENCE WITH VENETOCLAX-RITUXIMAB COMBINATION IN SOUTHERN ITALY.
EHA Library, stefano molica, 325411
MANAGEMENT OF PATIENTS WITH CHRONIC LYMPHOCYTIC LEUKEMIA AND ARTERIAL HYPERTENSION WHO ARE ON IBRUTINIB THERAPY.
EHA Library, Elena Emelina, 325413
NEUTROPHIL EXTRACELLULAR TRAPS ARE INCREASED IN CHRONIC MYELOID LEUKEMIA AND ARE DIFFERENTIALLY AFFECTED BY TYROSINE KINASE INHIBITORS
EHA Library, Alona Telerman, 325415
TNF-MEDIATED CML CELL SURVIVAL RESISTS TKI TREATMENT AND THIS CAN BE TARGETED BY IKK2-INHIBITION
EHA Library, Marlena Bütow, 325417
ANALYSIS OF MRNA AND DNA LEVEL OF ATYPICAL BCR-ABL1 TRANSCRIPTS IN CML PATIENTS OUTLINED AN ELIGIBILITY FOR TKI STOPPING
EHA Library, Katerina Machova, 325421
ANALYSIS OF MYELOID MUTATIONS IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA AND THEIR ASSOCIATION WITH ADVERSE EVENTS AND RELAPSE AFTER DISCONTINUATION.
EHA Library, Adrian Segura Díaz, 325422
NEGATIVE PROGNOSTIC IMPACT OF HIGH-RISK ADDITIONAL CYTOGENETIC ABNORMALITIES IN ADDITION TO THE ELTS IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Camille C.B. Kockerols, 325426
TREATMENT-FREE REMISSION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE FOLLOWING FRONTLINE NILOTINIB: RESULTS FROM JALSG N-STOP216
EHA Library, Naoto Takahashi, 325427
TREATMENT-FREE REMISSION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE FOLLOWING FRONTLINE DASATINIB: RESULTS FROM JALSG D-STOP216
EHA Library, Yosuke Minami, 325428
COMPARISON OF THE SOKAL AND EUTOS LONG-TERM SURVIVAL SCORES IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA RECEIVING TYROSINE KINASE INHIBITORS
EHA Library, Xiaoshuai Zhang, 325429
ASCIMINIB RESPONSES IN PONATINIB-PRETREATED PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Alejandro Luna, 325430
OUTCOMES BEFORE AND AFTER DOSE REDUCTION IN PATIENTS WITH NEWLY DIAGNOSED CHRONIC MYELOID LEUKEMIA RECEIVING BOSUTINIB OR IMATINIB
EHA Library, Michael W Deininger, 325431
FRONTLINE TREATMENT APPROACHES FOR CML IN MYELOID BLAST PHASE: A SINGLE-CENTER EXPERIENCE OVER 2 DECADES
EHA Library, Kapil Saxena, 325436
FRENCH REAL–LIFE OBSERVATIONAL STUDY 'TOPASE' EVALUATING SAFETY AND EFFICACY OF PONATINIB CONFIRMS INDUCTION OF DEEP MOLECULAR RESPONSES IN 110 RESISTANT OR INTOLERANT CML PATIENTS
EHA Library, Ali Turhan, 325439
WITHDRAWAL SYNDROME AFTER TYROSINE KINASE INHIBITORS DISCONTINUATION IN PATIENTS WITH CHRONIC MYELOID LEUKEMIA
EHA Library, Anna Petrova, 325440
FIRST INTERIM RESULTS OF THE RUSSIAN PROSPECTIVE STUDY OF REDUCTION AND DISCONTINUATION TREATMENT OF TKI (READIT) IN CHRONIC MYELOID LEUKEMIA PATIENTS WITH DEEP MOLECULAR RESPONSE
EHA Library, Margarita Gurianova, 325441
A SURVEY OF HEALTHCARE PROFESSIONALS IN THE UNITED KINGDOM TO DESCRIBE CURRENT PATHWAYS AND MANAGEMENT PRACTICES IN CHRONIC MYELOID LEUKAEMIA: THE ADAPT CML SURVEY
EHA Library, Adam Mead, 325442
COMPLEX MODES OF INHERITANCE IN HEREDITARY RED BLOOD CELL DISORDERS: A CASE SERIES STUDY OF 155 PATIENTS
EHA Library, Roberta Russo, 325448
BASELINE CHARACTERISTICS BY AGE OF A GLOBAL COHORT OF PATIENTS DIAGNOSED WITH PYRUVATE KINASE DEFICIENCY – A DESCRIPTIVE ANALYSIS FROM THE PEAK REGISTRY
EHA Library, Paola Bianchi, 325451
EARLY-ONSET OSTEOPENIA AND OSTEOPOROSIS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY
EHA Library, Hanny Al-Samkari, 325452
IMPACT OF OLIPUDASE ALFA ENZYME REPLACEMENT THERAPY ON PULMONARY, VISCERAL AND HEMATOLOGIC MANIFESTATIONS OF ACID SPHINGOMYELINASE DEFICIENCY: 1-YEAR RESULTS OF CLINICAL TRIALS IN CHILDREN AND ADULTS
EHA Library, Maurizio Scarpa, 325454
BONE MINERAL DENSITY IS STABLE IN ADULTS WITH PYRUVATE KINASE DEFICIENCY RECEIVING LONG-TERM TREATMENT WITH MITAPIVAT
EHA Library, Hanny Al-Samkari, 325456
SEVERE NEONATAL HAEMOLYTIC ANAEMIA AND SPHEROCYTIC-ELLYPTOCYTOSIS PHENOTYPE DUE TO THE INTERACTION OF THREE NOVEL SPTA1 MUTATIONS
EHA Library, Joan-Lluis Vives-Corrons, 325458
PYRUVATE KINASE DEFICIENCY IN THE RUSSIAN FEDERATION: AN OVERVIEW OF CLINICAL CHARACTERISTICS AND MOLECULAR DEFECTS.
EHA Library, Ekaterina Cherniak, 325459
CLINICAL FEATURES AND TREATMENT RESPONSES IN PEDIATRIC PATIENTS WITH WARM ANTIBODY IMMUNE HEMOLYTIC ANEMIA
EHA Library, Yesim Oymak, 325464
FACIT-FATIGUE SUBSCALE OUTCOMES FROM AN ONGOING PHASE 2, OPEN-LABEL STUDY OF THE PHOSPHATIDYLINOSITOL 3-KINASE DELTA (PI3KΔ) INHIBITOR PARSACLISIB IN PATIENTS WITH AUTOIMMUNE HEMOLYTIC ANEMIA (AIHA)
EHA Library, Fabrizio Pane, 325466
USE OF AN NGS PANEL FOR DE DIAGNOSIS OF HEREDITARY HEMOLYTIC ANEMIAS
EHA Library, Irene Zamanillo, 325468
MORTALITY AMONG VETERANS WITH A DIAGNOSIS OF PYRUVATE KINASE DEFICIENCY: A REAL-WORLD STUDY USING US VETERANS HEALTH ADMINISTRATION DATA
EHA Library, Erin Zagadailov, 325470

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