CLONAL HAEMOPOIESIS OF INDETERMINATE POTENTIAL AND MYELOPROLIFERATIVE DISEASE ARE ASSOCIATED WITH INCREASED EPIGENETIC AGE
EHA Library, Kristina Kirschner, 293953
UNSUPERVISED FLOWSOM ANALYSIS OF CLASSICAL FLOW CYTOMETRY PANELS SELF-GENERATES DISCRETE CELL SUBSETS OF NORMAL BONE MARROW.
EHA Library, Marie Christine Béné, 293954
THE BET INHIBITOR CPI203 PROMOTES EX VIVO EXPANSION OF CORD BLOOD LONG-TERM REPOPULATING HSCS AND MEGAKARYOCYTES
EHA Library, George Adigbli, 293955
IMPORTANT ROLE OF SKIN MESENCHYMAL STEM CELL SUBSETS IN NORMAL AND LEUKEMIC STEM CELL PROLIFERATION
EHA Library, Lakshmi Sandhow, 293956
CONDITIONAL EXPRESSION OF HOXA9 IN A HUMAN PLURIPOTENT STEM CELL DERIVED MODEL OF HEMATOPOIESIS.
EHA Library, Emma Collins, 293957
GENERATION OF HUMANIZED BONE MARROW-LIKE NICHE FOR LEUKEMIC XENOTRANSPLANTATION IN MICE: COMPARISON OF BIOMATERIALS
EHA Library, Martin Culen, 293958
THE IMBALANCED CYTOKINE PROFILE IN PATIENTS WITH PRE-LEUKEMIA
EHA Library, Amalie Bach Nielsen, 293959
PARKINSON'S DISEASE IS NOT ASSOCIATED WITH CLONAL HAEMATOPOIESIS
EHA Library, William DUNN, 293960
INHIBITION OF THE ANTI-APOPTOTIC PROTEIN MCL-1 SEVERELY SUPPRESSES HUMAN HEMATOPOIESIS
EHA Library, Miriam Erlacher, 293961
TUMOR-ASSOCIATED SIGNS OF A BONE MARROW HEMATOPOIETIC NICHE IN PATIENTS WITH MULTIPLE MYELOMA AFTER THERAPY
EHA Library, Natalya Semenova, 293962
A PHASE 1 STUDY OF CT103A, A FULLY HUMAN BCMA TARGETING CAR T CELL, IN SUBJECTS WITH RELAPSED/REFRACTORY MULTIPLE MYELOMA
EHA Library, Chunrui Li, 293963
ALLELE-SPECIFIC CRISPR/CAS9 GENE-EDITING STRATEGIES FOR ELANE MUTATIONS IN PRIMARY HSPCS OF SEVERE CONGENITAL NEUTROPENIA PATIENTS
EHA Library, Masoud Nasri, 293964
EFFICIENT CORRECTION OF HAX1 MUTATIONS IN PRIMARY HSPCS OF SEVERE CONGENITAL NEUTROPENIA PATIENTS USING CRISPR/CAS9 GENE-EDITING
EHA Library, Malte Ritter, 293965
A FLEXIBLE ISOGENEIC HUMANIZED MOUSE MODEL TO ASSESS CAR T CELL HEMATOLOGIC TOXICITY REVEALS MARROW-INDUCED CAR T CELL DYSFUNCTION.
EHA Library, Jacob Appelbaum, 293966
NPM1-MUTATED AML IS SUSCEPTIBLE TO SPECIFIC T CELLS DERIVED FROM NPM1 AND OTHER IMMUNOGENIC ANTIGENS AND IMMUNE RESPONSES INCREASE BY IMMUNE CHECKPOINT MANIPULATION
EHA Library, Jochen Greiner, 293967
T CELL ENGAGING BISPECIFIC ANTIBODIES GENERATED FROM A NOVEL, LARGE AND DIVERSE CD3 PANEL DEMONSTRATE FUNCTIONALITY UNCOUPLED FROM AFFINITY
EHA Library, Pieter Fokko Van Loo, 293968
CORD BLOOD DERIVED NK CELLS AS AN ATTRACTIVE OPTION TO ENHANCE THE EFFICACY OF CART CELL THERAPY
EHA Library, Mireia Bachiller, 293969
CLONAL TRACKING OF HEMATOPOIETIC RECONSTITUTION DYNAMICS AFTER BONE MARROW OR MOBILIZED PERIPHERAL BLOOD STEM CELL GENE THERAPY
EHA Library, Scala Serena, 293970
COMPARATIVE ANALYSES OF NKP30 CAR REDIRECTED HUMAN TCR-POSITIVE AND TCR-KNOCKDOWN T LYMPHOCYTES FOR CELLULAR IMMUNOTHERAPY
EHA Library, Sedigheh Givi, 293972
DEEP CHARACTERIZATION OF MBIL21 EX VIVO-EXPANDED NK CELLS USING MASS CYTOMETRY, FUNCTIONAL ASSAYS, AND RNA SEQUENCING ESTABLISHES PRODUCT CONSISTENCY ACROSS DIFFERENT MANUFACTURING SITES AND SYSTEMS
EHA Library, Dean A Lee, 293973
HIGHLY EFFICIENT THERAPEUTIC GENOME EDITING OF HEMATOPOIETIC STEM AND PROGENITOR CELLS TO CURE SICKLE CELL DISEASE AND THALASSEMIA
EHA Library, Han Verhagen, 293974
DEVELOPMENT OF A HUMANISED IMMUNOCOMPETENT MOUSE MODEL TO STUDY THE RELAPSE VACCINE DCP-001
EHA Library, Satwinder Kaur Singh, 293975
CHIMERIC ANTIGEN RECEPTOR (CAR)-MODIFIED NATURAL KILLER (NK) CELLS: PRECISION TOOLS FOR CANCER IMMUNOTHERAPY
EHA Library, Michael Morgan, 293976
DUAL FUNCTIONING, HUMAN CHROMATIN INSULATORS INCORPORATED IN LENTI-VIRAL VECTORS; A PLATFORM FOR OVERCOMING CURRENT LIMITATIONS OF HEMATOPOIETIC STEM CELL (HSC) GENE THERAPY
EHA Library, Penelope Georgia Papayanni, 293977
MULTI-TECHNIQUE FOLLOW-UP OF LYMPHOMA PATIENTS UNDERGOING COMMERCIAL CAR-T CELL THERAPY: EXPERIENCE FROM A SINGLE CENTRE
EHA Library, Rebeca Bailén, 293978
BETIBEGLOGENE AUTOTEMCEL (LENTIGLOBIN) IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA AND Β0/Β0, B+IVS-I-110/B+IVS-I-110, OR Β0/B+IVS-I-110 GENOTYPES: UPDATED RESULTS FROM THE HGB-212 STUDY
EHA Library, Evangelia Yannaki, 293980
CAR T-CELL THERAPY CAN IMPROVE THE OUTCOME OF RELAPSED/REFRACTORY DOUBLE-HIT LYMPHOMA
EHA Library, Jia Wei, 293981
GENE THERAPY WITH THE LENTIVIRAL VECTOR TNS9.3.55 PRODUCES LONG-TERM IMPROVEMENT IN SEVERE ß-THALASSEMIA
EHA Library, Simona Raso, 293982
ELIMINATION OF MULTI-DRUG RESISTANT HEMATOLOGICAL MALIGNANT CELLS RESULTING IN CURE USING NON-ENGRAFTING INTENTIONALLY MISMATCHED IL-2 ACTIVATED DONOR LYMPHOCYTES
EHA Library, Shimon Slavin, 293983
RECENT PROGRESS IN THE DEVELOPMENT OF AMT-061 (ETRANACOGENE DEZAPARVOVEC) FOR PERSONS WITH SEVERE OR MODERATELY SEVERE HEMOPHILIA B
EHA Library, Wolfgang Miesbach, 293984
OUTCOMES OF ANTI-CD19 CAR-T CELL THERAPY FOR TRANSFORMED NON FOLLICULAR LYMPHOMA
EHA Library, Lucía Rubio Lopes-Garcia, 293985
A METANALYSES OF THE WORLDWIDE EXPERIENCE OF AUTOLOGOUS HEMATOPOIETIC STEM CELL GENE THERAPY FOR MONOGENIC DISORDERS
EHA Library, Francesca Tucci, 293986
GENE THERAPY FOR FANCONI ANEMIA: A REPORT ON OUTCOMES IN NINE PATIENTS
EHA Library, Shameel Shafqat, 293987
FEASIBILITY OF ALLOGENEIC NATURAL KILLER CELLS, MG4101 IN COMBINATION WITH RITUXIMAB IN PATIENTS WITH RELAPSED OR REFRACTORY NON-HODGKIN LYMPHOMAS; A PHASE 1, OPEN-LABEL, MULTICENTER STUDY
EHA Library, Dok Hyun Yoon, 293988
TMTV CORRELATES WITH EARLY PROGRESSION (EP) AFTER CD19 CAR T-CELL THERAPY IN PATIENTS WITH RELAPSED/REFRACTORY DIFFUSE LARGE B-CELL LYMPHOMA (R/R DLBCL)
EHA Library, Sophie Bernard, 293989
GRANULOCYTE COLONY STIMULATING FACTOR (GCSF) ADMINISTRATION DOES NOT AFFECT PREVALENCE AND SEVERITY OF CRS, ICANS NOR OUTCOME IN PATIENTS WITH R/R LARGE B CELLS LYMPHOMAS TREATED BY CD19 CAR-T
EHA Library, Eugenio Galli, 293990
ENTECAVIR PROPHYLAXIS FOR HEPATITIS B VIRUS REACTIVATION IN PATIENTS WITH CAR T-CELL THERAPY
EHA Library, Liang Huang, 293991
REFRACTORY HEMOPHAGOCYTIC LYMPHOHISTIOCYTOSIS/MACROPHAGE-ACTIVATION SYNDROME (HLH/MAS) FOLLOWING TREATMENT WITH TISAGENLECLEUCEL FOR REFRACTORY B-CELL LYMPHOMA.
EHA Library, Ignacio Gómez-Centurión, 293992
IMMUNOLOGY-ONCOLOGY (I-O) DRUGS IN THE TREATMENT STRATEGIES FOR RELAPSE AFTER ANTI-CD19 CAR T CELLS IN PATIENTS WITH REFRACTORY/RELAPSED LARGE B CELL LYMPHOMA
EHA Library, Roberta Di Blasi, 293993
CD19-SPECIFIC CAR-T CELL THERAPY FOR RELAPSED/REFRACTORY NON B-CELL ACUTE LEUKEMIA WITH CD19 EXPRESSION
EHA Library, Shuangyou Liu, 293994
HIGH-GRADE NEUROLOGICAL TOXICITY FOLLOWING CD19 CAR-T THERAPY: OUTCOMES FROM A SINGLE CENTRE EXPERIENCE
EHA Library, Strachan Mackenzie, 293995
CD19 CAR T-CELL THERAPY FOR RELAPSED/REFRACTORY DIFFUSE LARGE B-CELL LYMPHOMA - THE MUNICH REAL LIFE EXPERIENCE
EHA Library, Veit Bücklein, 293996
DICLOFENAC IN THE MANAGEMENT OF CYTOKINE RELEASE SYNDROME AFTER CAR-T INFUSION IN B-ALL PEDIATRIC PATIENTS
EHA Library, Sara Napolitano, 293997
START OF THE PROCESSING OF LYMPHAPHERESIS IN A HOSPITAL AND IMPACT ON THE GENERATION OF CAR-T IN THE PRODUCTION CENTER
EHA Library, María Liz Paciello Coronel, 293998
REFRACTORY SEVERE ICANS IN A PATIENT TREATED WITH AXICABTAGENE CILOLEUCEL SUBSEQUENTLY FOUND TO HAVE SUSPECTED CNS DISEASE.
EHA Library, Nikesh Chavda, 293999
INCIDENCE AND MANAGEMENT OF VASO-OCCLUSIVE CRISES IN PATIENTS WITH SICKLE CELL DISEASE: A COUNTRY AND AGE ANALYSIS OF THE INTERNATIONAL SICKLE CELL WORLD ASSESSMENT SURVEY (SWAY)
EHA Library, Ifeyinwa Osunkwo, 294000
INCREASED CEREBRAL PERFUSION IS COUNTERBALANCED BY ARTERIOVENOUS SHUNTING IN PATIENTS WITH SICKLE CELL DISEASE
EHA Library, Liza Afzali-Hashemi, 294001
MANAGEMENT AND OUTCOME OF PATIENTS TREATED FOR HYPERHAEMOLYSIS; 5 YEAR EXPERIENCE IN A SINGLE INSTITUTION
EHA Library, Monica Ragheb, 294002
MACRO- AND MICROVASCULAR ENDOTHELIAL DYSFUNCTION MODULATION BY VCAM1 HAPLOTYPES OF PEDIATRIC SICKLE CELL ANEMIA PATIENTS
EHA Library, Paula Faustino, 294003
PROGRESSIVE COGNITIVE DECLINE IN ADULTS WITH SICKLE CELL DISEASE (SCD): THE EFFECTS OF THE SOCIOCULTURAL BACKGROUND AND CEREBRAL ATROPHY
EHA Library, Bruno D Benites, 294004
CELL-DERIVED MICROPARTICULES AND CYTOKINES PROFILE IN SICKLE CELL CHRONIC VASCULAR DISEASE IN SUB-SAHARAN AFRICA
EHA Library, Abdoul Karim Dembele, 294005
EPIDEMIOLOGY AND DISEASE BURDEN OF SCD IN FRANCE: A DESCRIPTIVE STUDY BASED ON A FRENCH NATIONWIDE CLAIMS DATABASE
EHA Library, Henri Leleu, 294006
IDENTIFICATION OF NON-COVALENT MODIFIERS OF HB S WITH A NOVEL HEMOGLOBIN BINDING SITE
EHA Library, Kelly Knee, 294007
USE OF OPIOIDS IN PATIENTS WITH SICKLE CELL DISEASE (SCD): A COUNTRY AND AGE ANALYSIS OF THE INTERNATIONAL SICKLE CELL WORLD ASSESSMENT SURVEY (SWAY)
EHA Library, Caterina Minniti, 294008
ADDING AZATHIOPRINE/HYDROXYUREA PRECONDITIONING TO ALEMTUZUMAB/TBI MAY REDUCE RISK OF GRAFT FAILURE IN MATCHED SIBLING DONOR ALLOGENEIC HSCT IN ADULT SICKLE CELL PATIENTS
EHA Library, Erfan Nur, 294009
INCIDENCE OF VASO-OCCLUSIVE CRISIS DOES NOT INCREASE WITH ACHIEVING HIGHER HEMOGLOBIN LEVELS ON VOXELOTOR TREATMENT OR AFTER DISCONTINUATION: ANALYSES OF THE HOPE STUDY
EHA Library, Elliott Vichinsky, 294010
POLYMORPHISMS IN GENES OF INNATE AND ADAPTIVE INFLAMMATORY RESPONSE MODULATE THE OCCURRENCE OF CLINICAL COMPLICATIONS IN PATIENTS WITH SICKLE CELL DISEASE
EHA Library, Karina Tozatto Maio, 294011
TRANSCRANIAL DOPPLER IN CHILDREN WITH SICKLE CELL DISEASE ON LONG-TERM FOLLOW-UP: A RETROSPECTIVE ANALYSIS
EHA Library, Ilaria Liguoro, 294012
AUTOIMMUNE DISEASE IS ASSOCIATED WITH GREATER RISK OF CO-MORBIDITY AMONG TEENS AND ADULTS IN THE SICKLE CELL DISEASE IMPLEMENTATION CONSORTIUM
EHA Library, Julie Kanter, 294013
SURVIVAL AND CAUSES OF DEATH IN A CAUCASIAN COHORT OF SICKLE CELL SYNDROMES PATIENTS
EHA Library, Gian Luca Forni, 294014
PHASE 1 SINGLE (SAD) AND MULTIPLE ASCENDING DOSE (MAD) STUDY OF THE SAFETY, PHARMACOKINETICS (PK) AND PHARMACODYNAMICS (PD) OF FT-4202, A PKR-ACTIVATOR, IN HEALTHY AND SICKLE CELL DISEASE SUBJECTS
EHA Library, Jeremie H. Estepp, 294015
STUDYING THE DETERMINANTS OF SICKLE CELL DISEASE VASCULOPATHY IN SUB-SAHARAN AFRICA : THE BIOCADRE STUDY
EHA Library, brigitte ranque, 294016
CORRELATION BETWEEN HEMOGLOBIN LEVELS AND TRANSCRANIAL DOPPLER VELOCITIES: A RETROSPECTIVE STOP 2 ANALYSIS IN CHILDREN WITH SICKLE CELL DISEASE
EHA Library, Jenifer H. Voeks, 294017
CONCOMITANT HYDROXYUREA AND VOXELOTOR: RESULTS FROM THE HOPE STUDY
EHA Library, Russell Ware, 294018
APPLICABILITY OF TWO METHODS FOR ESTIMATING AND ONE METHOD FOR MEASURING GLOMERULAR FILTRATION RATE IN SICKLE CELL ANEMIA PATIENTS IN CLINICAL PRACTICE
EHA Library, Samuel Souza Medina, 294019
GLOMERULAR FILTRATION RATE MEASURED BY 51-CR EDTA IN ADULT PATIENTS WITH SICKLE CELL DISEASE (SS AND SΒ0 THALASSEMIA): COMPARISON WITH EQUATIONS TO ESTIMATE RENAL FUNCTION.
EHA Library, Jhonny Manuel Carranza, 294020
EVIDENCE OF INEFFECTIVE ERYTHROPOIESIS IN SICKLE CELL DISEASE: THE ROLE OF FETAL HEMOGLOBIN AND HYPOXIA
EHA Library, Sara El Hoss, 294021
MITOCHONDRIA RETENTION IN MATURE RED BLOOD CELLS IN SICKLE CELL DISEASE
EHA Library, Suella Martino, 294022
PATIENT AND HEALTHCARE PROFESSIONAL PERCEPTIONS OF SICKLE CELL DISEASE IMPACT ON DAILY LIFE, SYMPTOM BURDEN AND TREATMENT: RESULTS FROM THE INTERNATIONAL SICKLE CELL WORLD ASSESSMENT SURVEY (SWAY)
EHA Library, Cassandra Trimnell, 294023
CORRELATION OF VOXELOTOR EXPOSURE WITH HEMOGLOBIN RESPONSE AND MEASURES OF HEMOLYSIS IN PATIENTS FROM THE HOPE STUDY
EHA Library, Jo Howard, 294024
RENAL COMPLICATIONS AND PREDICTIONS OF CHRONIC RENAL DISEASE IN NEWBORN COHORT OF PATIENTS WITH HOMOZYGOUS SICKLE CELL DISEASE
EHA Library, Muriel Soriano, 294025
COMPLICATIONS OF FLUID REPLACEMENT THERAPY (HYPERHYDRATION) IN SICKLE CELL PATIENTS DURING VASO-OCCLUSIVE PAINFUL CRISIS
EHA Library, Aafke Gaartman, 294026
MANUAL ERITHROEXCHANGE IN SICKLE CELL DISEASE: MULTICENTER VALIDATION OF A PROTOCOL INCLUDING A FORMULA TO CALCULATE THE VOLUME TO EXCHANGE
EHA Library, Gian Luca Forni, 294027
INDIVIDUALIZED CARE PLANS IMPROVE HEALTH CARE UTILIZATION AND LENGTH OF STAY IN ADULTS WITH SICKLE CELL DISEASE
EHA Library, Caterina Minniti, 294028
GENETIC MODIFIERS OF SICKLE CELL DISEASE IN PATIENTS TREATED WITH HYDROXYUREA
EHA Library, Pierre Allard, 294029
CARDIAC MAGNETIC RESONANCE IDENTIFYING PATIENTS WITH HEART FAILURE IN SICKLE CELL DISEASE: A SINGLE-INSITUTION EXPERIENCE
EHA Library, Monica Bawor, 294030
INTERNATIONAL DONOR SEARCHES OF HUMAN LEUKOCYTE ANTIGEN MATCHED UNRELATED DONORS FOR PATIENTS WITH SICKLE CELL DISEASE FROM DIFFERENT GEOGRAPHIC ORIGINS
EHA Library, Karina Tozatto Maio, 294031
ASSESSMENT OF LONGER-TERM EFFICACY AND SAFETY IN THE PHASE 3 BELIEVE TRIAL OF LUSPATERCEPT TO TREAT ANEMIA IN PATIENTS (PTS) WITH Β-THALASSEMIA
EHA Library, Ali T. Taher, 294032
OUTCOMES OF HAPLO-CORD TRANSPLANTATION IN CHILDREN WITH BETA THALASSEMIA MAJOR
EHA Library, Uet Yu, 294033
OXIDATIVE STRESS IN NON-TRANSFUSION DEPENDENT THALASSEMIA: A JOURNEY FROM NADPH OXIDASES TO CYTOCHROME P450
EHA Library, Rayan Bou-Fakhredin, 294034
UNDERLYING Α-GLOBIN GENE DEFECTS DEFINE COMPLICATION-FREE SURVIVAL IN PATIENTS WITH HEMOGLOBINOPATHY H
EHA Library, Polyxeni Delaporta, 294035
IMPACT OF ABO INCOMPATIBILITY ON OUTCOMES AFTER UNRELATED DONOR HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR BETA THALASSEMIA MAJOR
EHA Library, Yuelin He, 294036
DIFFERENT SOURCE OF PBSC IMPROVED THE OUTCOME OF SIBLING AND UNRELATED UMBILICAL CORD BLOOD STEM CELL TRANSPLANTATION IN TM::84 CASES REPORT
EHA Library, Xiaoqin Feng, 294037
EFFECTIVENESS OF HYDROXYUREA THERAPY: A 15 YEAR EXPERIENCE OF THALASSEMIA MANAGEMENT WITHOUT BLOOD TRANSFUSION
EHA Library, Saqib Hussain, 294038
SERUM ERYTHROFERRONE LEVELS AND ERYTHROFERRONE TO FERRITIN RATIO (ERY/FER) ARE PROMISING NEW LABORATORY MARKERS OF IRON OVERLOAD IN PATIENTS WITH BETA-THALASSEMIA INTERMEDIA
EHA Library, Walaa Elsalakawy, 294039
DONOR LYMPHOCYTE INFUSION IMPROVES TRANSPLANT OUTCOME OF UMBILICAL CORD BLOOD FROM HLA-IDENTICAL SIBLING DONORS IN THALASSEMIA MAJOR
EHA Library, Jianyun Liao, 294040
ASSESSMENT OF ATHEROSCLEROSIS IN PERIPHERAL AND CENTRAL CIRCULATION IN ADULT Β THALASSEMIA INTERMEDIA PATIENTS BY COLOR DOPPLER U/S. EGYPTIAN EXPERIENCE.
EHA Library, Noha El Husseiny, 294041
AUTOIMMUNE HEMOLYTIC ANEMIA AFTER HAPLOIDENTICAL HEMATOPOIETICSTEM CELL TRANSPLANTATION IN CHILDREN WITH Β- THALASSEMIA MAJOR
EHA Library, Yue Li, 294042
EFFECT OF HBB GENOTYPE ON SURVIVAL IN A COHORT OF TRANSFUSION-DEPENDENT THALASSEMIA PATIENTS IN CYPRUS
EHA Library, Paul Telfer, 294043
FOG1-DEPENDENT TRANSCRIPTIONAL NETWORK INVOLVES GLUCOSE METABOLIC REGULATION OF ERYTHROID CELLS
EHA Library, Tohru Fujiwara, 294044
MITAPIVAT (AG-348) LONG-TERM SAFETY AND EFFICACY IN PYRUVATE KINASE DEFICIENCY: 3-YEAR RESULTS OF THE DRIVE PK STUDY
EHA Library, Rachael Grace, 294045
MISSENSE OR NON MISSENSE: IS THAT THE QUESTION?
EHA Library, Beatriz González Fernández, 294046
SURVIVAL IN AUTOIMMUNE HEMOLYTIC ANEMIA REMAINS POOR
EHA Library, Dennis Lund Hansen, 294047
INCREASED HEMOLYSIS MARKERS ARE PREDICTORS OF MORTALITY IN PATIENTS WITH COLD AGGLUTININ DISEASE—REAL-WORLD EVIDENCE FROM A UNITED STATES ELECTRONIC HEALTH RECORD DATABASE
EHA Library, Jun Su, 294049
SECONDARY DEFICIENCY OF PYRUVATE KINASE AND ALTERED RED CELL METABOLISM IN HEREDITARY XEROCYTOSIS CAUSED BY PIEZO1 AND KCNN4 DEFECTS
EHA Library, Minke Rab, 294050
SIROLIMUS IS EFFECTIVE FOR RELAPSED/REFRACTORY AUTOIMMUNE CYTOPENIAS: A MULTICENTER STUDY
EHA Library, Jiang Ji, 294051
DEEP INTRONIC PATHOGENETIC VARIANTS IN THE FECH GENE CAUSE ERYTHROPOIETIC PROTOPORPHYRIA THROUGH PSEUDOEXON ACTIVATION DURING PRE-MRNA SPLICING
EHA Library, Elena Di Pierro, 294052
IMPACT OF INTRAVASCULAR HEMOLYSIS AND MULTITREATMENT ON THROMBOSIS OCCURRENCE IN AUTOIMMUNE HEMOLYTIC ANEMIA
EHA Library, Bruno Fattizzo, 294053
IMPROVING THE EMA BINDING TEST BY USING COMMERCIALLY AVAILABLE FLUORESCENT BEADS
EHA Library, Andreas Glenthøj, 294054
NEWBORN LYSOSOMAL STORAGE SCREENING BY NEXT GENERATION SEQUENCING
EHA Library, Laura López De, 294055

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