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LYMPHOCYTE COUNT EFFECT ON EFFICACY AND SAFETY OF SINGLE AGENT ORAL SELINEXOR IN PATIENTS WITH RELAPSED/REFRACTORY DIFFUSE LARGE B-CELL LYMPHOMA (DLBCL): A POST-HOC ANALYSIS FROM PHASE 2B SADAL STUDY
Author(s): ,
Michael Schuster
Affiliations:
Stony Brook University,Stony Brook,United States
,
Miguel Canales
Affiliations:
2Hospital Universitario La Paz, Madrid,Spain
,
Jason Westin
Affiliations:
University of Texas MD Anderson Cancer Center,Houston,United States
,
Josee Zijlstra
Affiliations:
Amsterdam UMC, Vrije Universiteit, Cancer Center,Amsterdam,Netherlands
,
George Follows
Affiliations:
Addenbrooke’s Hospital,Cambridge,United Kingdom
,
Reem Karmali
Affiliations:
Northwestern Medical Faculty Foundation Division Hematology Oncology,Chicago,United States
,
Nagesh Kalakonda
Affiliations:
University of Liverpool,Liverpool,United Kingdom
,
Andre Goy
Affiliations:
John Theurer Cancer Center, Hackensack University Medical Center,Hackensack,United States
,
Rene-Oliver Casasnovas
Affiliations:
Hématologie Clinique and INSERM 1231, CHU Dijon,Dijon,France
,
Joost S.P. Vermaat
Affiliations:
LUMC,Leiden,Netherlands
,
Eric Van den Neste
Affiliations:
Cliniques Universitaires Saint-Luc,Brussels,Belgium
,
Sylvian Choquet
Affiliations:
Hôpital Pitié Salpêtrière,Paris,France
,
Catherine Thieblemont
Affiliations:
APHP, Saint-Louis Hospital & Diderot University, University de Paris,Paris,France
,
Federica Cavallo
Affiliations:
Department of Molecular Biotechnologies and Health Sciences, Division of Hematology, University of Torino,Turin,Italy
,
Fatima De La Cruz Vincete
Affiliations:
Hospital Universitario Virgen del Rocio,Sevilla,Spain
,
Brian Hill
Affiliations:
Cleveland Clinic,Cleveland,United States
,
Herve Tilly
Affiliations:
Centre Henri Becquerel,Rouen,France
,
Shireen Kassam
Affiliations:
King's College Hospital,London,United Kingdom
,
Ulrich Jaeger
Affiliations:
Medical University of Vienna,Vienna,Austria
,
Ronit Gurion
Affiliations:
Rabin MC and TA University,Petah Tiqwa,Israel
,
Paolo Caimi
Affiliations:
UH Cleveland Medical Center,Cleveland,United States
,
Peter Martin
Affiliations:
Weill Cornell/New York Presbyterian,New York,United States
,
Andrew Davies
Affiliations:
Cancer Research UK/NIHR Experimental Cancer Medicines Centre, University of Southampton,Southampton,United Kingdom
,
Sonali Smith
Affiliations:
University of Chicago,Chicago,United States
,
Graham Collins
Affiliations:
Oxford University Hospitals NHS Foundation Trust,Oxford,United Kingdom
,
Fritz Offner
Affiliations:
UZ Gent,Gent,Belgium
,
Gilles Salles
Affiliations:
CHU Lyon Sud,Pierre-Bénite,France
,
Xiwen Ma
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Kelly Corona
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Jean-Richard Saint-Martin
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Kamal Chamoun
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Jatin Shah
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Sharon Shacham
Affiliations:
Karyopharm Therapeutics,Newton,United States
,
Michael Kauffman
Affiliations:
Karyopharm Therapeutics,Newton,United States
Marie Maerevoet
Affiliations:
Institut Jules Bordet,Brussels,Belgium
EHA Library. Schuster M. 06/09/21; 325290; EP530
Michael Schuster
Michael Schuster
Contributions
Abstract
Presentation during EHA2021: All e-poster presentations will be made available as of Friday, June 11, 2021 (09:00 CEST) and will be accessible for on-demand viewing until August 15, 2021 on the Virtual Congress platform.

Abstract: EP530

Type: E-Poster Presentation

Session title: Aggressive Non-Hodgkin lymphoma - Clinical

Background
Selinexor is a first-in-class, oral Selective Inhibitor of Nuclear Export (SINE) compound that blocks XPO1, forcing the nuclear retention and functional activation of tumor suppressor proteins including p53, p73, FOXO, IkB and Rb. The phase 2b SADAL study included 134 patients with relapsed or refractory DLBCL with single agent selinexor twice weekly. The overall response rate (ORR) was 29.1%, median duration of response (DOR) 9.3 months and the median overall survival (OS) 9 months. Based on these data, selinexor was approved by the US FDA for the treatment of relapsed or refractory DLBCL, de novo or transformed from follicular lymphoma. Studies have shown that a lower absolute lymphocyte counts (ALC) is a strong prognostic factor for reduced PFS and OS in patients with DLBCL.

Aims
To performed post-hoc analyses of results from the SADAL study to determine the impact of baseline ALC on the efficacy and safety of selinexor.

Methods
The SADAL study was multi-center, open-label Phase 2b study that enrolled patients with DLBCL treated with 2-5 lines of therapy treated with oral selinexor 60mg twice weekly until disease progression. Patients may have recurrence after stem cell therapy (SCT) or were not candidates for SCT. The primary endpoint was ORR, and other endpoints included DOR, OS and safety assessments. For the current analysis, patients were divided into categories based on baseline ALC (≥1000/µL and <1000/µL) in order to compare outcomes.

Results
Of the 134 patients enrolled in the SADAL study, 61 (46%) had baseline ALC of ≥1000/µL and 71 (53%) had levels <1000/µL. The majority of patients in both groups were <65 years old, 79% and 72%, respectively. In this population, de novo and transformed DLBCL accounted for 82% and 18% with ALC ≥1000/µL and 72% and 28% in patients with ALC <1000/µL and, respectively. DLBCL subtype was also similarly distributed among patients with GCB and non-GCB in those with ALC ≥1000/µL (51% and 43%) and in those with ALC <1000/µL (44% and 55%), respectively.

The ORR in patients who had baseline ALC ≥1000/µL was 32.8% compared to 25.4% for ALC <1000/µL (p=0.455; complete responses (CR) rates were 13.1% vs 14.1% respectively. The median DOR in patients who had ALC ≥1000/µL was 23.0 months compared to 4.9 months in patients with ALC <1000/µL (p=0.228). The median PFS were 3.6 and 2.1 and median OS were 15.5 and 7.6 months in patients with ALC ≥1000/µL and <1000/µL, respectively (p=0.129; p=0.013).


The most common grade ≥3 treatment-related adverse events (AEs) for patients with ALC ≥1000/µL and <1000/µL were thrombocytopenia (42.6% vs. 38.0%), nausea (6.6% vs. 4.2%) and fatigue (9.8% vs. 11.3%). The incidence of treatment-related serious AEs and AEs leading to discontinuation in patients who had a lymphocyte count of ≥1000/µL vs <1000/µL were 26.2% vs. 16.9% and 11.5% vs. 4.2%, respectively; these differences may have been related to duration of response.

Conclusion
In this post-hoc analysis in patients enrolled in SADAL with relapsed/refractory DLBCL treated with single agent oral selinexor, those with baseline ALC ≥1000/µL had a ALC a slightly higher ORR (33% vs 25%) but similar CR rates and PFS to those with ALC<1000/µL.  Significantly longer overall survival was observed in patients with higher baseline ALC, and responses in these patients trended to longer duration. While consistent with many reports in the literature regarding the poor prognosis of baseline ALC <1000/µL, these results need to be confirmed in larger studies with longer follow up.

Keyword(s):

Presentation during EHA2021: All e-poster presentations will be made available as of Friday, June 11, 2021 (09:00 CEST) and will be accessible for on-demand viewing until August 15, 2021 on the Virtual Congress platform.

Abstract: EP530

Type: E-Poster Presentation

Session title: Aggressive Non-Hodgkin lymphoma - Clinical

Background
Selinexor is a first-in-class, oral Selective Inhibitor of Nuclear Export (SINE) compound that blocks XPO1, forcing the nuclear retention and functional activation of tumor suppressor proteins including p53, p73, FOXO, IkB and Rb. The phase 2b SADAL study included 134 patients with relapsed or refractory DLBCL with single agent selinexor twice weekly. The overall response rate (ORR) was 29.1%, median duration of response (DOR) 9.3 months and the median overall survival (OS) 9 months. Based on these data, selinexor was approved by the US FDA for the treatment of relapsed or refractory DLBCL, de novo or transformed from follicular lymphoma. Studies have shown that a lower absolute lymphocyte counts (ALC) is a strong prognostic factor for reduced PFS and OS in patients with DLBCL.

Aims
To performed post-hoc analyses of results from the SADAL study to determine the impact of baseline ALC on the efficacy and safety of selinexor.

Methods
The SADAL study was multi-center, open-label Phase 2b study that enrolled patients with DLBCL treated with 2-5 lines of therapy treated with oral selinexor 60mg twice weekly until disease progression. Patients may have recurrence after stem cell therapy (SCT) or were not candidates for SCT. The primary endpoint was ORR, and other endpoints included DOR, OS and safety assessments. For the current analysis, patients were divided into categories based on baseline ALC (≥1000/µL and <1000/µL) in order to compare outcomes.

Results
Of the 134 patients enrolled in the SADAL study, 61 (46%) had baseline ALC of ≥1000/µL and 71 (53%) had levels <1000/µL. The majority of patients in both groups were <65 years old, 79% and 72%, respectively. In this population, de novo and transformed DLBCL accounted for 82% and 18% with ALC ≥1000/µL and 72% and 28% in patients with ALC <1000/µL and, respectively. DLBCL subtype was also similarly distributed among patients with GCB and non-GCB in those with ALC ≥1000/µL (51% and 43%) and in those with ALC <1000/µL (44% and 55%), respectively.

The ORR in patients who had baseline ALC ≥1000/µL was 32.8% compared to 25.4% for ALC <1000/µL (p=0.455; complete responses (CR) rates were 13.1% vs 14.1% respectively. The median DOR in patients who had ALC ≥1000/µL was 23.0 months compared to 4.9 months in patients with ALC <1000/µL (p=0.228). The median PFS were 3.6 and 2.1 and median OS were 15.5 and 7.6 months in patients with ALC ≥1000/µL and <1000/µL, respectively (p=0.129; p=0.013).


The most common grade ≥3 treatment-related adverse events (AEs) for patients with ALC ≥1000/µL and <1000/µL were thrombocytopenia (42.6% vs. 38.0%), nausea (6.6% vs. 4.2%) and fatigue (9.8% vs. 11.3%). The incidence of treatment-related serious AEs and AEs leading to discontinuation in patients who had a lymphocyte count of ≥1000/µL vs <1000/µL were 26.2% vs. 16.9% and 11.5% vs. 4.2%, respectively; these differences may have been related to duration of response.

Conclusion
In this post-hoc analysis in patients enrolled in SADAL with relapsed/refractory DLBCL treated with single agent oral selinexor, those with baseline ALC ≥1000/µL had a ALC a slightly higher ORR (33% vs 25%) but similar CR rates and PFS to those with ALC<1000/µL.  Significantly longer overall survival was observed in patients with higher baseline ALC, and responses in these patients trended to longer duration. While consistent with many reports in the literature regarding the poor prognosis of baseline ALC <1000/µL, these results need to be confirmed in larger studies with longer follow up.

Keyword(s):

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